Imai Kohsuke, Zhu Yi, Revy Patrick, Morio Tomohiro, Mizutani Shuki, Fischer Alain, Nonoyama Shigeaki, Durandy Anne
Institut National de la Santé et de la Recherche Médicale (INSERM) Unité 429, Hôpital Necker-Enfants Malades, Paris, France.
Clin Immunol. 2005 Jun;115(3):277-85. doi: 10.1016/j.clim.2005.02.003.
Autosomal recessive form of hyper-IgM syndrome type 2 (AR-HIGM2) is secondary to mutations affecting both alleles of AICDA gene encoding activation-induced cytidine deaminase, characterized by defects of immunoglobulin class switch recombination (CSR) and somatic hypermutation (SHM) in most of the patients. We herein report the immunological phenotype of seven patients carrying a single heterozygous R190X mutation in AICDA. Variable defect in in vivo CSR inherited as an autosomal dominant (AD) trait strongly suggests that this heterozygous AICDA mutation causes HIGM (AD-HIGM2). In AD-HIGM2 B cells, CSR was consistently found impaired in vitro. However, in contrast to AR-HIGM2, the CSR-induced double-stranded DNA breaks in the switch region of IgM heavy chain gene were detected. The SHM frequency in V regions of IgM heavy chain gene in B cells was normal in all (but one patient). The characteristics of the AD-HIGM2 phenotype indicate that the AID C-terminal region may be involved in DNA repair machinery required for CSR.
2型高IgM综合征的常染色体隐性形式(AR-HIGM2)继发于影响编码活化诱导胞苷脱氨酶的AICDA基因两个等位基因的突变,其特征是大多数患者存在免疫球蛋白类别转换重组(CSR)和体细胞超突变(SHM)缺陷。我们在此报告7例携带AICDA基因单个杂合R190X突变患者的免疫表型。作为常染色体显性(AD)性状遗传的体内CSR可变缺陷强烈提示该杂合AICDA突变导致HIGM(AD-HIGM2)。在AD-HIGM2 B细胞中,体外持续发现CSR受损。然而,与AR-HIGM2不同,在IgM重链基因转换区检测到CSR诱导的双链DNA断裂。所有患者(除1例患者外)B细胞中IgM重链基因V区的SHM频率正常。AD-HIGM2表型的特征表明AID C末端区域可能参与CSR所需的DNA修复机制。