Conley Mary Ellen, Dobbs A Kerry, Farmer Dana M, Kilic Sebnem, Paris Kenneth, Grigoriadou Sofia, Coustan-Smith Elaine, Howard Vanessa, Campana Dario
Department of Pediatrics, University of Tennessee College of Medicine, Memphis, Tennessee 38163, USA.
Annu Rev Immunol. 2009;27:199-227. doi: 10.1146/annurev.immunol.021908.132649.
Sophisticated genetic tools have made possible the identification of the genes responsible for most well-described immunodeficiencies in the past 15 years. Mutations in Btk, components of the pre-B cell and B cell receptor (lambda5, Igalpha, Igbeta), or the scaffold protein BLNK account for approximately 90% of patients with defects in early B cell development. Hyper-IgM syndromes result from mutations in CD40 ligand, CD40, AID, or UNG in 70-80% of affected patients. Rare defects in ICOS or CD19 can result in a clinical picture that is consistent with common variable immunodeficiency, and as many as 10% of patients with this disorder have heterozygous amino acid substitutions in TACI. For all these disorders, there is considerable clinical heterogeneity in patients with the same mutation. Identifying the genetic and environmental factors that influence the clinical phenotype may enhance patient care and our understanding of normal B cell development.
在过去15年里,先进的基因工具使得识别导致大多数已充分描述的免疫缺陷的基因成为可能。Btk、前B细胞和B细胞受体的组成部分(λ5、Igα、Igβ)或支架蛋白BLNK中的突变约占早期B细胞发育缺陷患者的90%。70 - 80%的受影响患者的高IgM综合征是由CD40配体、CD40、AID或UNG中的突变引起的。ICOS或CD19中的罕见缺陷可导致与常见可变免疫缺陷一致的临床表现,多达10%的这种疾病患者在TACI中有杂合氨基酸替代。对于所有这些疾病,具有相同突变的患者存在相当大的临床异质性。识别影响临床表型的遗传和环境因素可能会改善患者护理并增进我们对正常B细胞发育的理解。