Servicio de Hematología, Hospital Clínico Universitario de Valladolid, Valladolid, Spain.
Eur J Haematol. 2012 Jul;89(1):37-41. doi: 10.1111/j.1600-0609.2012.01799.x.
The myeloproliferative neoplasms displaying a PDGFRB rearrangement are rare diseases derived from a haematopoietic stem cell. The goals of the study were to assess the incidence of these disorders and to define the clinical and biological characteristics as well as the response to the imatinib therapy.
A total of 556 patients with myeloproliferative neoplasms were studied by means of molecular cytogenetics.
The incidence of myeloproliferative neoplasms (MPN) with PDGFRB rearrangement was low (10 cases, 1.8% of all MPN). Most of the patients showed moderate anaemia (median Hb was 10.0 gr/dL; range from 7.5 to 13 g/dL), leukocytosis (median white blood cells was 21.7 × 10(9) /L with a range from 4 to 43 × 10(9) /L) and eosinophilia (median circulating eosinophils was 2.4 × 10(9) /L with a range of 1.1-5.7 × 10(9) /L) with a median of bone marrow infiltration cells displaying PDGFRB rearrangement of 55% (range, 37-85%). In three cases, a t(5;12) was observed while two patients showed rearrangements of 17q21 region. In two cases, a del(5)(q31) was observed. Most of the patients responded to standard dosage of imatinib, and the response was maintained in the time in those patients with a follow-up higher than 9 years.
The incidence of patients with PDGFRB rearrangement is low. These patients showed leukocytosis with eosinophilia and anaemia. The efficacy of imatinib therapy in patients showing PDGFRB rearrangement is high. For this reason, in all patients with MPN without any other molecular aberration, PDGFRB rearrangement should be ascertained.
伴有 PDGFRB 重排的骨髓增殖性肿瘤是一种源于造血干细胞的罕见疾病。本研究的目的是评估这些疾病的发生率,并定义其临床和生物学特征以及对伊马替尼治疗的反应。
通过分子细胞遗传学方法对 556 例骨髓增殖性肿瘤患者进行研究。
伴有 PDGFRB 重排的骨髓增殖性肿瘤(MPN)的发生率较低(10 例,占所有 MPN 的 1.8%)。大多数患者表现为中度贫血(中位数血红蛋白为 10.0g/dL;范围为 7.5-13g/dL)、白细胞增多(中位数白细胞为 21.7×10(9)/L,范围为 4-43×10(9)/L)和嗜酸性粒细胞增多(中位数循环嗜酸性粒细胞为 2.4×10(9)/L,范围为 1.1-5.7×10(9)/L),骨髓浸润细胞中 PDGFRB 重排中位数为 55%(范围为 37-85%)。在 3 例中观察到 t(5;12),2 例患者显示 17q21 区域的重排。在 2 例中观察到 del(5)(q31)。大多数患者对标准剂量的伊马替尼有反应,并且在随访时间超过 9 年的患者中,反应得以维持。
伴有 PDGFRB 重排的患者发生率较低。这些患者表现为白细胞增多伴嗜酸性粒细胞增多和贫血。在伴有 PDGFRB 重排的患者中,伊马替尼治疗的疗效较高。因此,在所有无其他分子异常的 MPN 患者中,应确定 PDGFRB 重排。