Weng Zhihui, Kong Chi-Wing, Ren Lihuan, Karakikes Ioannis, Geng Lin, He Jiaozi, Chow Maggie Zi Ying, Mok Chong Fai, Chan Harvey Y S, Webb Sarah E, Keung Wendy, Chow Howard, Miller Andrew L, Leung Anskar Y H, Hajjar Roger J, Li Ronald A, Chan Camie W
1 Stem Cell & Regenerative Medicine Consortium, LKS Faculty of Medicine, The University of Hong Kong , Pokfulam, Hong Kong .
Stem Cells Dev. 2014 Jul 15;23(14):1704-16. doi: 10.1089/scd.2013.0509. Epub 2014 Apr 22.
Self-renewable human pluripotent stem cells (hPSCs) serve as a potential unlimited ex vivo source of human cardiomyocytes (CMs) for cell-based disease modeling and therapies. Although recent advances in directed differentiation protocols have enabled more efficient derivation of hPSC-derived CMs with an efficiency of ∼50%-80% CMs and a final yield of ∼1-20 CMs per starting undifferentiated hPSC, these protocols are often not readily transferrable across lines without first optimizing multiple parameters. Further, the resultant populations are undefined for chamber specificity or heterogeneous containing mixtures of atrial, ventricular (V), and pacemaker derivatives. Here we report a highly cost-effective and reproducibly efficient system for deriving hPSC-ventricular cardiomyocytes (VCMs) from all five human embryonic stem cell (HES2, H7, and H9) and human induced PSC (hiPSC) (reprogrammed from human adult peripheral blood CD34(+) cells using nonintegrating episomal vectors) lines tested. Cardiogenic embryoid bodies could be formed by the sequential addition of BMP4, Rho kinase inhibitor, activin-A, and IWR-1. Spontaneously contracting clusters appeared as early as day 8. At day 16, up to 95% of cells were cTnT(+). Of which, 93%, 94%, 100%, 92%, and 92% of cardiac derivatives from HES2, H7, H9, and two iPSC lines, respectively, were VCMs as gauged by signature ventricular action potential and ionic currents (INa(+)/ICa,L(+)/IKr(+)/IKATP(+)); Ca(2+) transients showed positive chronotropic responses to β-adrenergic stimulation. Our simple, cost-effective protocol required the least amounts of reagents and time compared with others. While the purity and percentage of PSC-VCMs were comparable to a recently published protocol, the present yield and efficiency with a final output of up to 70 hPSC-VCMs per hPSC was up to 5-fold higher and without the need of performing line-specific optimization. These differences were discussed. The results may lead to mass production of hPSC-VCMs in bioreactors.
自我更新的人多能干细胞(hPSC)可作为人心肌细胞(CM)潜在的无限体外来源,用于基于细胞的疾病建模和治疗。尽管定向分化方案最近取得了进展,能够更有效地获得hPSC衍生的CM,效率约为50%-80%,每个起始未分化hPSC的最终产量约为1-20个CM,但这些方案在不首先优化多个参数的情况下通常不易在不同细胞系间转移。此外,所得细胞群体的腔室特异性不明确,或者包含心房、心室(V)和起搏细胞衍生物的异质混合物。在此,我们报告了一种高度经济高效且可重复的系统,用于从测试的所有五种人类胚胎干细胞(HES2、H7和H9)和人类诱导多能干细胞(hiPSC)(使用非整合附加型载体从人类成人外周血CD34(+)细胞重编程而来)系中衍生hPSC-心室心肌细胞(VCM)。通过依次添加BMP4、Rho激酶抑制剂、激活素A和IWR-1可形成心肌胚状体。早在第8天就出现了自发收缩的细胞簇。在第16天,高达95%的细胞为心肌肌钙蛋白T(cTnT)阳性。其中,根据特征性心室动作电位和离子电流(INa(+)/ICa,L(+)/IKr(+)/IKATP(+))判断,来自HES2、H7、H9和两个hiPSC系的心脏衍生物分别有93%、94%、100%、92%和92%为VCM;Ca(2+)瞬变对β-肾上腺素能刺激表现出正性变时反应。与其他方案相比,我们简单、经济高效的方案所需试剂和时间最少。虽然PSC-VCM的纯度和百分比与最近发表的方案相当,但目前的产量和效率高达每个hPSC最终产出70个hPSC-VCM,高出多达5倍,且无需进行细胞系特异性优化。对这些差异进行了讨论。这些结果可能会导致在生物反应器中大规模生产hPSC-VCM。