从β-地中海贫血成纤维细胞生成的未分化诱导多能干细胞可通过CRISPR/Cas9进行高效基因校正。 - Suppr

Naïve Induced Pluripotent Stem Cells Generated From β-Thalassemia Fibroblasts Allow Efficient Gene Correction With CRISPR/Cas9.

作者信息

Yang Yuanyuan, Zhang Xiaobai, Yi Li, Hou Zhenzhen, Chen Jiayu, Kou Xiaochen, Zhao Yanhong, Wang Hong, Sun Xiao-Fang, Jiang Cizhong, Wang Yixuan, Gao Shaorong

出版信息

Stem Cells Transl Med. 2016 Feb;5(2):267. doi: 10.5966/sctm.2015-0157erratum.

DOI:10.5966/sctm.2015-0157erratum

PMID:26819338

原文链接:https://pmc.ncbi.nlm.nih.gov/articles/PMC4729555/

Abstract

摘要

https://cdn.ncbi.nlm.nih.gov/pmc/blobs/2308/4729555/858b9dd405a9/sctm_20150157erratum_f2b.jpg

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Naïve Induced Pluripotent Stem Cells Generated From β-Thalassemia Fibroblasts Allow Efficient Gene Correction With CRISPR/Cas9.

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