Jurek Przemysław M, Zabłocki Konrad, Waśko Urszula, Mazurek Maciej P, Otlewski Jacek, Jeleń Filip
Department of Protein Engineering, Faculty of Biotechnology, University of Wrocław, Poland.
Int J Nanomedicine. 2017 Apr 11;12:2941-2950. doi: 10.2147/IJN.S125231. eCollection 2017.
Compounds that recognize and strongly bind to molecular targets are one of the cornerstones of modern pharmaceutics. Work has been ongoing for the past 25 years on the therapeutic use of aptamers, nucleic acid molecules, whose three-dimensional structure is the result of interactions between complementary base pairs. The aptamers selection methods allow the oligonucleotides which bind the molecular target in its native environment to be quickly isolated from a large library of random oligonucleotides. The possibilities presented for aptamers in the field of targeted therapy require the application of effective carriers to counter the renal clearance effect and/or functional cargo to exert therapeutic action if the aptamer is only used as a targeting moiety. Lately, a material gaining ground in biomedical research is iron oxide particles, which exhibit a superparamagnetic characteristic at nanoscale levels. This allows the iron oxide nanoparticles to convert external magnetic energy into heat, a mechanism known as hyperthermy, and efficiently supports conventional oncological treatment. In this study, we describe an experimentally confirmed functional model of targeted anticancer hyperthermia therapy. Using the systematic evolution of ligands by exponential enrichment technique, we selected a DNA aptamer that specifically binds to the extracellular domain of recombinant fibroblast growth factor receptor type-1 (FGFR1) with a nanomolar dissociation constant. The chosen target plays an important role in many crucial cellular processes and is also considered a candidate protein that is involved in tumor initiation, survival and progression. Next, we combined the selected aptamer with iron oxide nanoparticles to produce aptamer superparamagnetic conjugates (ASCs). Finally, we found that targeted ASCs selectively destroy FGFR1-overexpressing human osteosarcoma cells U2OS upon magnetic field irradiation.
能够识别并强烈结合分子靶点的化合物是现代制药学的基石之一。在过去25年里,人们一直在研究适体(核酸分子)的治疗用途,其三维结构是互补碱基对之间相互作用的结果。适体筛选方法能够从大量随机寡核苷酸文库中快速分离出在天然环境中与分子靶点结合的寡核苷酸。如果仅将适体用作靶向部分,那么在靶向治疗领域中,适体所展现的可能性需要应用有效的载体来对抗肾脏清除效应和/或功能性货物以发挥治疗作用。最近,一种在生物医学研究中逐渐流行的材料是氧化铁颗粒,它在纳米尺度上表现出超顺磁性特征。这使得氧化铁纳米颗粒能够将外部磁能转化为热量,这一机制被称为热疗,并有效地支持传统的肿瘤治疗。在本研究中,我们描述了一种经实验证实的靶向抗癌热疗功能模型。利用指数富集配体系统进化技术,我们筛选出一种DNA适体,它能以纳摩尔解离常数特异性结合重组成纤维细胞生长因子受体1型(FGFR1)的细胞外结构域。所选择的靶点在许多关键细胞过程中发挥着重要作用,并且也被认为是一种参与肿瘤起始、存活和进展的候选蛋白。接下来,我们将筛选出的适体与氧化铁纳米颗粒结合,制备出适体超顺磁性缀合物(ASC)。最后,我们发现靶向ASC在磁场照射下能选择性地破坏过表达FGFR1的人骨肉瘤细胞U2OS。