Efficient therapy of Pompe disease by an acid α-glucosidase conjugate.
作者信息
Park Kinam
机构信息
Purdue University Biomedical Engineering and PharmaceuticsWest Lafayette, IN 47907, USA.
出版信息
J Control Release. 2018 Jan 10;269:441-442. doi: 10.1016/j.jconrel.2017.12.010.
Abstract
摘要
相似文献
1
Efficient therapy of Pompe disease by an acid α-glucosidase conjugate.
J Control Release. 2018 Jan 10;269:441-442. doi: 10.1016/j.jconrel.2017.12.010.
2
Low-frequency enzyme replacement therapy in late-onset Pompe disease.
Muscle Nerve. 2013 Apr;47(4):612-3. doi: 10.1002/mus.23658. Epub 2013 Jan 16.
3
Ptosis in Pompe disease: common genetic background in infantile and adult series.
J Neuroophthalmol. 2010 Dec;30(4):389-90. doi: 10.1097/WNO.0b013e3181f9a923.
4
Long-term enzyme-replacement therapy (ERT) with alglucosidase alfa: Evolution of two siblings with juvenile late-onset Pompe disease.
J Neurol Sci. 2015 Nov 15;358(1-2):459-60. doi: 10.1016/j.jns.2015.08.007. Epub 2015 Aug 7.
5
Efficient therapy for refractory Pompe disease by mannose 6-phosphate analogue grafting on acid α-glucosidase.
J Control Release. 2018 Jan 10;269:15-23. doi: 10.1016/j.jconrel.2017.10.043. Epub 2017 Nov 3.
6
Enzyme replacement in Pompe disease with an alpha-glucosidase-low density lipoprotein complex.
Birth Defects Orig Artic Ser. 1980;16(1):415-23.
7
Improvement of bilateral ptosis on higher dose enzyme replacement therapy in Pompe disease.
J Neuroophthalmol. 2010 Jun;30(2):165-6. doi: 10.1097/WNO.0b013e3181ce162a.
8
Infantile Pompe disease: clinical and genetic characteristics with an experience of enzyme replacement therapy.
J Child Neurol. 2012 Mar;27(3):319-24. doi: 10.1177/0883073811420295. Epub 2011 Sep 22.
9
Oral delivery of Acid Alpha Glucosidase epitopes expressed in plant chloroplasts suppresses antibody formation in treatment of Pompe mice.
Plant Biotechnol J. 2015 Oct;13(8):1023-32. doi: 10.1111/pbi.12413. Epub 2015 Jun 5.
10
Acid alpha-glucosidase deficiency (Pompe disease).
Curr Neurol Neurosci Rep. 2007 Jan;7(1):71-7. doi: 10.1007/s11910-007-0024-4.
Zotero 插件