Computational Medicine Center, Thomas Jefferson University, Philadelphia, Pennsylvania.
Ocular Oncology Service, Wills Eye Hospital, Thomas Jefferson University, Philadelphia, Pennsylvania.
Pigment Cell Melanoma Res. 2020 Jan;33(1):52-62. doi: 10.1111/pcmr.12810. Epub 2019 Aug 16.
Uveal melanoma (UVM) is the most common primary intraocular malignancy in adults. With over 50% of patients developing metastatic disease, there is an unmet need for improved diagnostic and therapeutic options. Efforts to understand the molecular biology of the disease have revealed several markers that correlate with patient prognosis, including the copy number of chromosome 3, genetic alterations in the BAP1, EIF1AX and SF3B1 genes, and other transcriptional features. Here, we expand upon previous reports by comprehensively characterizing the short RNA-ome in 80 primary UVM tumor samples. In particular, we describe a previously unseen complex network involving numerous regulatory molecules that comprise microRNA (miRNAs), novel UVM-specific miRNA loci, miRNA isoforms (isomiRs), and tRNA-derived fragments (tRFs). Importantly, we show that the abundance profiles of isomiRs and tRFs associate with various molecular phenotypes, metastatic disease, and patient survival. Our findings suggest deep involvement of isomiRs and tRFs in the disease etiology of UVM. We posit that further study and characterization of these novel molecules will improve understanding of the mechanisms underlying UVM, and lead to the development of new diagnostic and therapeutic approaches.
葡萄膜黑色素瘤(UVM)是成年人中最常见的原发性眼内恶性肿瘤。超过 50%的患者发生转移性疾病,因此需要改进诊断和治疗选择。为了了解疾病的分子生物学,已经发现了一些与患者预后相关的标志物,包括染色体 3 的拷贝数、BAP1、EIF1AX 和 SF3B1 基因的遗传改变,以及其他转录特征。在这里,我们通过全面描述 80 个原发性 UVM 肿瘤样本的短 RNA 组,扩展了以前的报告。特别是,我们描述了一个以前看不见的复杂网络,涉及许多调节分子,包括 microRNA(miRNAs)、新型 UVM 特异性 miRNA 基因座、miRNA 异构体(isomiRs)和 tRNA 衍生片段(tRFs)。重要的是,我们表明 isomiRs 和 tRFs 的丰度谱与各种分子表型、转移性疾病和患者生存相关。我们的研究结果表明,isomiRs 和 tRFs 深度参与了 UVM 的疾病发病机制。我们假设对这些新型分子的进一步研究和表征将提高对 UVM 发病机制的理解,并导致新的诊断和治疗方法的发展。