Keogh Steven J, Dalle Jean-Hugues, Admiraal Rick, Pulsipher Michael A
Cancer Centre for Children, The Children's Hospital at Westmead, Westmead, NSW, Australia.
Hôpital Robert Debré, GHU AP-HP. Nord Université de Paris, Paris, France.
Front Pediatr. 2022 Jan 6;9:805189. doi: 10.3389/fped.2021.805189. eCollection 2021.
Serotherapy comprising agents such as anti-thymocyte globulin, anti-T-lymphocyte globulin, and the anti-CD52 monoclonal antibody alemtuzumab is used widely to reduce the incidence of graft-versus-host disease (GvHD) after paediatric haematopoietic stem cell transplantation (HSCT). The outcome of transplants using matched unrelated donors now approaches that of matched sibling donors. This is likely due to better disease control in recipients, the use of donors more closely human-leukocyte antigen (HLA)-matched to recipients, and more effective graft-versus-host disease (GvHD) prophylaxis. The price paid for reduced GvHD is slower immune reconstitution of T cells and thus more infections. This has led to studies looking to optimise the amount of serotherapy used. The balance between prevention of GvHD on one side and prevention of infections and relapse on the other side is quite delicate. Serotherapy is given with chemotherapy-/radiotherapy-based conditioning prior to HSCT. Due to their long half-lives, agents used for serotherapy may be detectable in patients well after graft infusion. This exposes the graft-infused T cells to a lympholytic effect, impacting T-cell recovery. As such, excessive serotherapy dosing may lead to no GvHD but a higher incidence of infections and relapse of leukaemia, while under-dosing may result in a higher chance of serious GvHD as immunity recovers more quickly. Individualised dosing is being developed through studies including retrospective analyses of serotherapy exposure, population pharmacokinetic modelling, therapeutic drug monitoring in certain centres, and the development of dosing models reliant on factors including the patient's peripheral blood lymphocyte count. Early results of "optimal" dosing strategies for serotherapy and conditioning chemotherapy show promise of improved overall survival.
包含抗胸腺细胞球蛋白、抗T淋巴细胞球蛋白和抗CD52单克隆抗体阿仑单抗等药物的血清疗法被广泛用于降低儿童造血干细胞移植(HSCT)后移植物抗宿主病(GvHD)的发生率。使用匹配的无关供体进行移植的结果现在已接近匹配的同胞供体移植的结果。这可能是由于受者的疾病控制更好、使用与受者人类白细胞抗原(HLA)匹配度更高的供体以及更有效的移植物抗宿主病(GvHD)预防措施。为降低GvHD而付出的代价是T细胞免疫重建较慢,因此感染更多。这导致了旨在优化血清疗法使用量的研究。一方面预防GvHD与另一方面预防感染和复发之间的平衡相当微妙。血清疗法在HSCT前与基于化疗/放疗的预处理联合使用。由于用于血清疗法的药物半衰期较长,在移植输注后很长时间仍可在患者体内检测到。这使移植的T细胞受到淋巴细胞溶解作用,影响T细胞恢复。因此,血清疗法剂量过大可能导致无GvHD,但感染和白血病复发的发生率更高,而剂量不足可能导致严重GvHD的几率更高,因为免疫恢复更快。通过包括血清疗法暴露的回顾性分析、群体药代动力学建模、某些中心的治疗药物监测以及依赖患者外周血淋巴细胞计数等因素的给药模型开发,正在制定个体化给药方案。血清疗法和预处理化疗的“最佳”给药策略的早期结果显示出改善总体生存率的前景。