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依伐卡托与泰他卡托和艾乐卡托联合治疗后囊性纤维化患者感染相关就诊和抗生素使用的快速减少。

The Rapid Reduction of Infection-Related Visits and Antibiotic Use Among People With Cystic Fibrosis After Starting Elexacaftor-Tezacaftor-Ivacaftor.

机构信息

Department of Internal Medicine, University of Iowa, Iowa City, Iowa, USA.

Department of Biostatistics, University of Iowa, Iowa City, Iowa, USA.

出版信息

Clin Infect Dis. 2022 Sep 30;75(7):1115-1122. doi: 10.1093/cid/ciac117.

Abstract

BACKGROUND

People with cystic fibrosis (CF) routinely suffer from recurrent sinopulmonary infections. Such infections require frequent courses of antimicrobials and often involve multidrug-resistant organisms. The goal of this study was to identify real-world evidence for the effectiveness of elexacaftor-tezacaftor-ivacaftor (ELX/TEZ/IVA) in decreasing infection-related visits and antimicrobial use in people with CF.

METHODS

Using IBM MarketScan data, we identified 389 enrollees with CF who began taking ELX/TEZ/IVA before 1 December 2019 and were enrolled from 1 July 2019 to 14 March 2020. We also identified a comparison population who did not begin ELX/TEZ/IVA during the study period. We compared the following outcomes in the 15 weeks before and after medication initiation: total healthcare visits, inpatient visits, infection-related visits, and antimicrobial prescriptions. We analyzed outcomes using both a case-crossover analysis and a difference-in-differences analysis, to control for underlying trends.

RESULTS

For the case-crossover analysis, ELX/TEZ/IVA initiation was associated with the following changes over a 15-week period: change in overall healthcare visit dates, -2.5 (95% confidence interval, -3.31 to -1.7); change in inpatient admissions, -0.16 (-.22 to -.10); change in infection-related visit dates, -0.62 (-.93 to -.31); and change in antibiotic prescriptions, -0.78 (-1.03 to -.54). Results from the difference-in-differences approach were similar.

CONCLUSIONS

We show a rapid reduction in infection-related visits and antimicrobial use among people with CF after starting a therapy that was not explicitly designed to treat infections. Currently, there are >30 000 people living with CF in the United States alone. Given that this therapy is effective for approximately 90% of people with CF, the impact on respiratory infections and antimicrobial use may be substantial.

摘要

背景

囊性纤维化(CF)患者经常遭受反复的鼻窦肺部感染。此类感染需要频繁使用抗生素治疗,并且常常涉及耐多药病原体。本研究的目的是确定真实世界证据,证明依伐卡托与泰比曲肽和艾美拉唑(ELX/TEZ/IVA)在减少 CF 患者感染相关就诊和抗生素使用方面的有效性。

方法

我们使用 IBM MarketScan 数据,确定了 389 名在 2019 年 12 月 1 日前开始服用 ELX/TEZ/IVA 的 CF 患者,并在 2019 年 7 月 1 日至 2020 年 3 月 14 日期间入组。我们还确定了一个在研究期间未开始服用 ELX/TEZ/IVA 的对照组。我们比较了药物起始前 15 周和后 15 周的以下结果:总医疗就诊次数、住院就诊次数、感染相关就诊次数和抗生素处方。我们使用病例交叉分析和差异分析来分析结果,以控制潜在趋势。

结果

对于病例交叉分析,ELX/TEZ/IVA 起始治疗与 15 周内的以下变化相关:总医疗就诊日期的变化,-2.5(95%置信区间,-3.31 至-1.7);住院入院的变化,-0.16(-0.22 至-0.10);感染相关就诊日期的变化,-0.62(-0.93 至-0.31);抗生素处方的变化,-0.78(-1.03 至-0.54)。差异分析的结果相似。

结论

我们发现,开始治疗后 CF 患者的感染相关就诊和抗生素使用迅速减少,而该治疗方案并非专门用于治疗感染。目前,仅在美国就有超过 30000 人患有 CF。鉴于该疗法对约 90%的 CF 患者有效,对呼吸道感染和抗生素使用的影响可能是巨大的。

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