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The first successful expanded compassionate use of Iptacopan in a patient with paroxysmal nocturnal hemoglobinuria.

作者信息

Han Bing, Ji Jiang, Zhang Bo, Bai Hua, Zhou Daobin, Feng Feng, Huang Yan, Zhu Huijuan, Chen Limeng, Wu Zhihong, Jiang Xiuchun, Li Xuemei, Jia Qing, Chang Qing, Pan Hui, Peng Hua, Zheng Wenting, Huang Hui, Chen Zheng, Yang Chen, Chen Miao, Du Bin, Zhang Shuyang

机构信息

Peking Union Medical College Hospital, Beijing, China.

出版信息

Ann Hematol. 2022 Nov;101(11):2537-2539. doi: 10.1007/s00277-022-04933-5. Epub 2022 Aug 15.

Abstract
摘要

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