Precision Immunology Institute, Department of Oncological Sciences, The Tisch Cancer Institute, Icahn School of Medicine at Mount Sinai, New York, NY 10029, USA.
Division of Hematology/Oncology, Tisch Cancer Institute, Icahn School of Medicine at Mount Sinai, New York, NY 10029, USA.
Int J Mol Sci. 2022 Dec 14;23(24):15907. doi: 10.3390/ijms232415907.
Acute myeloid leukemia (AML) is a hematological malignancy characterized by clonal expansion of stem and myeloid progenitor cells. Immunotherapy has revolutionized the care for other cancers such as solid tumors and lymphomas, and has the potential to effectively treat AML. There has been substantial progress in the developments of immunotherapeutic approaches for AML over the last several years, including the development of antibodies that further increase the innate immunogenicity of leukemia cells by the inhibition of NKG2D ligand-particularly MICA and MICB-shedding, chimeric proteins such as IL-15 superagonist that expand natural killer (NK) cells, blockers of immunologic checkpoints such as NKG2A, and chemicals that indirectly increase expression of immune stimulatory proteins in leukemia stem cells. Furthermore, cellular therapies have been designed to enable alloreactive immunity by allogeneic NK cells or target leukemia antigens such as mutated NPM1. These immunotherapeutic approaches have demonstrated remarkable efficacies in preclinical studies and have successfully transitioned to early phase clinical trials, to establish safety and initial signal of clinical activity. Here, we briefly discuss some of the most recent and impactful developments in the AML immunotherapy field and provide our perspectives for the future directions of this exciting and new therapeutic opportunity.
急性髓系白血病 (AML) 是一种血液系统恶性肿瘤,其特征是干细胞和髓系祖细胞的克隆性扩增。免疫疗法已经彻底改变了对实体瘤和淋巴瘤等其他癌症的治疗方式,并且有可能有效地治疗 AML。在过去几年中,AML 的免疫治疗方法取得了实质性的进展,包括开发了通过抑制 NKG2D 配体——特别是 MICA 和 MICB 的脱落来进一步增加白血病细胞固有免疫原性的抗体、IL-15 超级激动剂等嵌合蛋白来扩增自然杀伤 (NK) 细胞、免疫检查点抑制剂如 NKG2A 的阻断剂,以及能够间接增加白血病干细胞中免疫刺激蛋白表达的化学物质。此外,还设计了细胞疗法,通过同种异体 NK 细胞或靶向白血病抗原(如突变型 NPM1)来实现同种异体反应性免疫。这些免疫治疗方法在临床前研究中显示出显著的疗效,并成功地过渡到早期临床试验,以建立安全性和初步的临床活性信号。在这里,我们简要讨论了 AML 免疫治疗领域的一些最新和最有影响力的进展,并为这一令人兴奋的新治疗机会提供了我们的未来发展方向。