Department of Pathology and Laboratory Medicine, Memorial Sloan Kettering Cancer Center, New York, New York, USA.
Department of Pathology, Cleveland Clinic, Cleveland, Ohio, USA.
Genes Chromosomes Cancer. 2024 Jan;63(1):e23198. doi: 10.1002/gcc.23198. Epub 2023 Sep 2.
Composite hemangioendothelioma is a rare, locally aggressive, and rarely metastasizing vascular neoplasm which affects both children and adults. Recently, a number of gene fusions including YAP1::MAML2, PTBP1::MAML2, and EPC1::PHC2 have been detected in a small subset of cases with or without neuroendocrine expression. Herein, we present four additional cases with novel in-frame fusions. The cohort comprises two females and two males with a wide age range at diagnosis (24-80 years). Two tumors were deep involving the right brachial plexus and mediastinum, while the remaining were superficial (right plantar foot and abdominal wall). The size ranged from 1.5 to 4.8 cm in greatest dimension. Morphologically, all tumors had an admixture of at least two architectural patterns including retiform hemangioendothelioma, hemangioma, epithelioid hemangioendothelioma, or angiosarcoma. The tumors were positive for endothelial markers CD31 (3/3), ERG (4/4), and D2-40 (1/4, focal), while SMA was expressed in 2/3 highlighting the surrounding pericytes. Synaptophysin showed immunoreactivity in 2/3 cases. One patient had a local recurrence after 40 months, while two patients had no evidence of disease 4 months post-resection. Targeted RNA sequencing detected novel in-frame fusions in each of the cases: HSPG2::FGFR1, YAP1::FOXR1, ACTB::MAML2, and ARID1B::MAML2. The two cases with neuroendocrine expression occurred as superficial lesions and harbored YAP1::FOXR1 and ARID1B::MAML2 fusions. Our study expands on the molecular spectrum of this enigmatic tumor, further enhancing our current understanding of the disease.
复合型血管内皮细胞瘤是一种罕见的局部侵袭性、罕见转移的血管肿瘤,可影响儿童和成人。最近,在一小部分具有或不具有神经内分泌表达的病例中,检测到了多种基因融合,包括 YAP1::MAML2、PTBP1::MAML2 和 EPC1::PHC2。在此,我们介绍另外 4 例具有新型框内融合的病例。该队列包括 2 名女性和 2 名男性,诊断时年龄范围广泛(24-80 岁)。2 个肿瘤深在累及右侧臂丛和纵隔,而其余 2 个肿瘤为表浅(右足底和腹壁)。最大直径大小为 1.5-4.8cm。形态学上,所有肿瘤均至少存在两种混合结构模式,包括网状血管内皮细胞瘤、血管瘤、上皮样血管内皮细胞瘤或血管肉瘤。肿瘤均表达内皮标志物 CD31(3/3)、ERG(4/4)和 D2-40(1/4,局灶性),而 SMA 在 2/3 例中表达,突出周围的周细胞。突触素在 2/3 例中显示免疫反应性。1 例患者在 40 个月后出现局部复发,2 例患者在切除后 4 个月无疾病证据。靶向 RNA 测序在每个病例中均检测到新型框内融合:HSPG2::FGFR1、YAP1::FOXR1、ACTB::MAML2 和 ARID1B::MAML2。2 例具有神经内分泌表达的病例为表浅病变,携带 YAP1::FOXR1 和 ARID1B::MAML2 融合。本研究扩展了该神秘肿瘤的分子谱,进一步增强了我们对该疾病的现有认识。