Kanemoto Yoshiaki, Iwaki Miho, Sawada Takahiro, Nojiri Koki, Kurokawa Tomohiro, Tsutsumi Rino, Nagasawa Kazuo, Kato Shigeaki
Graduate School of Life Science and Technology, Iryo Sosei University, Iwaki, Fukushima, Japan.
Research Institute of Innovative Medicine, Tokiwa Foundation, Iwaki, Fukushima, Japan.
J Bone Metab. 2023 Aug;30(3):219-229. doi: 10.11005/jbm.2023.30.3.219. Epub 2023 Aug 31.
Vitamin D (VD) exerts a wide variety of biological actions in addition to its well-known roles in calcium homeostasis. Nutritional VD deficiency induces rachitic abnormalities in growing children and osteomalacia in adults, and it has been proposed to underlie the onset and development of multiple non-communicable chronic diseases. Therefore, the administration of VD or synthetic VD analogues represents a promising therapeutic strategy; indeed, VD and a VD agonist have shown clinical promise in mitigating osteoporosis and symptoms of insufficient calcium intake. However, even though high doses of VD analogues have shown pre-clinical efficacy against several diseases, including cancers, they have not yet had wide-spread clinical success. This difference may be due to limitation of clinical doses in light of the inherent calcemic action of VD. An approach to overcome this problem involves the development of VD analogues with lower calcemic activity, which could be administered in high doses to attenuate the onset and progress of disease. In a similar strategy, selective estrogen receptor modulators have had success as anti-osteoporosis drugs, and they have shown benefit for other estrogen target organs by serving as partial antagonists or agonists of estrogen receptor α. It is thus conceivable to generate synthetic partial antagonists or agonists for the VD receptor (VDR) that would exert beneficial effects on bone and other VD target organs. In this review, we discuss the molecular basis of the development of such synthetic VDR ligands from the viewpoint of roles of VDR in gene regulation.
维生素D(VD)除了在钙稳态中发挥众所周知的作用外,还具有多种生物学作用。营养性VD缺乏会导致儿童佝偻病和成人骨软化症,并且有人提出它是多种非传染性慢性病发病和发展的基础。因此,给予VD或合成VD类似物是一种有前景的治疗策略;事实上,VD和一种VD激动剂已在减轻骨质疏松症和钙摄入不足症状方面显示出临床前景。然而,尽管高剂量的VD类似物在包括癌症在内的几种疾病的临床前研究中已显示出疗效,但它们尚未在临床上广泛取得成功。这种差异可能是由于考虑到VD固有的血钙作用而限制了临床剂量。克服这一问题的一种方法是开发具有较低血钙活性的VD类似物,这种类似物可以高剂量给药以减轻疾病的发生和进展。类似地,选择性雌激素受体调节剂作为抗骨质疏松药物已取得成功,并且它们通过作为雌激素受体α的部分拮抗剂或激动剂,对其他雌激素靶器官也显示出益处。因此,可以设想生成对VD受体(VDR)起作用的合成部分拮抗剂或激动剂,它们将对骨骼和其他VD靶器官产生有益影响。在这篇综述中,我们从VDR在基因调控中的作用角度讨论此类合成VDR配体开发的分子基础。