Suppr超能文献

一例 4 岁女童进行核黄素治疗及人工耳蜗植入的病例报告:进行性听力损失和言语发育迟缓:Brown-Vialetto-Van Laere 综合征。

A Case Report of Riboflavin Treatment and Cochlear Implants in a 4-Year-Old Girl with Progressive Hearing Loss and Delayed Speech Development: Brown-Vialetto-Van Laere Syndrome.

机构信息

Oto-Rhino-Laryngology Surgery Clinic, World Hearing Center, Institute of Physiology and Pathology of Hearing, Kajetany, Poland.

Department of Teleaudiology and Screening, World Hearing Center, Institute of Physiology and Pathology of Hearing, Kajetany, Poland.

出版信息

Am J Case Rep. 2023 Oct 3;24:e940439. doi: 10.12659/AJCR.940439.

Abstract

BACKGROUND Brown-Vialetto-Van Laere (BVVL) syndrome is a rare autosomal recessive disorder caused by mutations in intestinal riboflavin transporter genes, resulting in a motor neuron disorder of childhood, which can be associated with sensorineural deafness. This report describes a 4-year-old Polish girl with progressive hearing loss and delayed speech development diagnosed with Brown-Vialetto-Van Laere syndrome who was treated with riboflavin (vitamin B2) and cochlear implants. CASE REPORT The case report concerns a girl from Poland who, at the age of 2 years 10 months, developed progressive atypical neurological symptoms of unknown etiology: ataxia of the upper and lower limbs, gait abnormalities, generalized muscle weakness, visual and hearing problems, and regression of speech development. A karyotype study (whole-exome sequencing) revealed alterations within SLC52A2, leading to the diagnosis of Brown-Vialetto-Van Laere syndrome and initiation of high-dose riboflavin treatment. As a 4-year-old child, she presented to the Institute of Physiology and Pathology of Hearing - World Hearing Center in Poland with progressive hearing loss and speech regression. Hearing tests revealed bilateral profound sensorineural hearing loss with auditory neuropathy. Surgical treatment was applied in the form of bilateral cochlear implantation. CONCLUSIONS This report shows the importance of genetic testing in infants who present with atypical symptoms or signs. In this case, the diagnosis of Brown-Vialetto-Van Laere syndrome resulted in timely correction of the genetic riboflavin (vitamin B2) deficiency and improved hearing following the use of cochlear implants.

摘要

背景

Brown-Vialetto-Van Laere(BVVL)综合征是一种罕见的常染色体隐性疾病,由肠道核黄素转运基因的突变引起,导致儿童运动神经元疾病,可伴有感觉神经性耳聋。本报告描述了一名 4 岁波兰女孩,她因进行性听力损失和言语发育迟缓被诊断为 Brown-Vialetto-Van Laere 综合征,接受了核黄素(维生素 B2)和人工耳蜗植入治疗。

病例报告

本病例报告涉及一名来自波兰的女孩,她在 2 岁 10 个月时出现了进行性、非典型的病因不明的神经症状:上下肢共济失调、步态异常、全身肌肉无力、视力和听力问题以及言语发育倒退。染色体组研究(外显子组测序)显示 SLC52A2 内的改变,导致诊断为 Brown-Vialetto-Van Laere 综合征,并开始进行高剂量核黄素治疗。4 岁时,她因进行性听力损失和言语退化到波兰生理学和听力病理学研究所-世界听力中心就诊。听力测试显示双侧重度感觉神经性听力损失伴听神经病。采用双侧人工耳蜗植入的手术治疗。

结论

本报告表明,对出现非典型症状或体征的婴儿进行基因检测非常重要。在本例中,Brown-Vialetto-Van Laere 综合征的诊断导致及时纠正了遗传性核黄素(维生素 B2)缺乏症,并在使用人工耳蜗植入后改善了听力。

https://cdn.ncbi.nlm.nih.gov/pmc/blobs/f14b/10560793/4e05ce09bdbf/amjcaserep-24-e940439-g001.jpg

文献AI研究员

20分钟写一篇综述,助力文献阅读效率提升50倍。

立即体验

用中文搜PubMed

大模型驱动的PubMed中文搜索引擎

马上搜索

文档翻译

学术文献翻译模型,支持多种主流文档格式。

立即体验