Université Libre de Bruxelles (ULB), Hôpital Universitaire de Bruxelles (H.U.B), Hôpital Erasme, Service de Gynécologie-Obstetrique, Clinique de Fertilité, Route de Lennik, 808, 1070, Brussels, Belgium.
Novafertil IVF Center, Konya, Turkey.
J Assist Reprod Genet. 2024 Feb;41(2):311-322. doi: 10.1007/s10815-023-03009-1. Epub 2024 Jan 5.
Women undergoing controlled ovarian hyperstimulation prior to in vitro fertilization (IVF) are treated using various protocols to induce multiple follicular growths. Complete failure of all oocytes to mature during IVF cycles is rare; however, it is a known cause of primary female infertility. Recently, pathogenic variations in a few genes have been identified in women with oocyte maturation defects; however, the underlying genetic causes remain largely unknown.This study included a Turkish family comprising three sisters with recurring oocyte maturation arrest at the germinal vesicle stage after multiple ovarian stimulations. Exome sequencing revealed a homozygous missense variant (c.1037C>T, p.Ala346Val) in the EPAB gene (also known as PABPC1L) in all three affected sisters, which was either absent or heterozygous in the unaffected family members. Functional experiments confirming the pathogenicity of the variant were performed by transfecting HEK293T cells and demonstrated the instability and increased rate of proteolysis of the mutated PABPC1L/EPAB protein. The identified variant, located in the well-conserved fourth RNA recognition motif (RRM4), in silico 3D modelling suggested changes in the physical properties of the pathogenic variant of PABPC1L/EPAB. Our findings validate PABPC1L/EPAB as an essential genetic contributor to the oocyte maturation process in humans and have direct implications for the genetic counselling of patients and their family members.
在体外受精 (IVF) 之前接受控制性卵巢超刺激的女性使用各种方案来诱导多个卵泡生长。在 IVF 周期中,所有卵子完全不成熟的情况很少见;然而,这是原发性女性不孕的已知原因。最近,在卵子成熟缺陷的女性中已经确定了少数几个基因的致病变异;然而,潜在的遗传原因在很大程度上仍然未知。本研究包括一个土耳其家庭,该家庭由三个在多次卵巢刺激后处于生发泡阶段的卵母细胞成熟反复停滞的姐妹组成。外显子组测序显示,所有受影响的姐妹均存在 EPAB 基因(也称为 PABPC1L)中的纯合错义变异 (c.1037C>T,p.Ala346Val),而未受影响的家庭成员中该变异要么缺失,要么为杂合子。通过转染 HEK293T 细胞进行的功能实验证实了该变异的致病性,并表明突变的 PABPC1L/EPAB 蛋白的不稳定性和蛋白水解率增加。该鉴定的变异位于高度保守的第四个 RNA 识别基序 (RRM4) 中,计算机 3D 建模提示 PABPC1L/EPAB 致病性变异体的物理性质发生变化。我们的发现证实了 PABPC1L/EPAB 是人类卵母细胞成熟过程中的一个重要遗传贡献者,并直接影响患者及其家庭成员的遗传咨询。