Woodard DaNae R, Ayyagari Radha
Department of Ophthalmology, Shiley Eye Institute, University of California San Diego, San Diego, CA, USA.
Adv Exp Med Biol. 2025;1468:75-79. doi: 10.1007/978-3-031-76550-6_13.
The membrane-frizzled related protein (MFRP) is a retinal pigment epithelium (RPE) and ciliary epithelium-expressed gene of unknown function. Interest in MFRP stems from clinical manifestations that range from acute-angle closure glaucoma to microphthalmia and Retinitis pigmentosa in patients with MFRP mutations. Furthermore, the genetic ablation of Mfrp in mice results in an early-onset retinal disease with visible degeneration around 1mo of age and primary rod photoreceptor loss. Yet, little is known regarding the exact role of MFRP in the RPE, its underlying contribution to pathology, and the impacted mechanisms at the early stages of MFRP-related disease. This review presents a current overview of MFRP studies and poses outstanding questions that are crucial for understanding the involvement of MFRP in early-onset retinal degeneration. Such insight could pave the way for deciphering the molecular mechanisms associated with MFRP that are impacted during early stages in the retina, offering the potential to translate this knowledge into determining similarities and differences in mechanisms involved in late-stage retinal diseases.
膜卷曲相关蛋白(MFRP)是一种在视网膜色素上皮(RPE)和睫状体上皮中表达但功能未知的基因。对MFRP的关注源于其突变患者中从急性闭角型青光眼到小眼症和色素性视网膜炎等一系列临床表现。此外,小鼠中Mfrp基因的缺失会导致一种早发性视网膜疾病,在约1月龄时出现明显的变性,并伴有原发性视杆光感受器丧失。然而,关于MFRP在RPE中的具体作用、其对病理学的潜在贡献以及MFRP相关疾病早期阶段的受影响机制,我们知之甚少。本综述介绍了MFRP研究的当前概况,并提出了一些悬而未决的问题,这些问题对于理解MFRP在早发性视网膜变性中的作用至关重要。这样的见解可能为破译视网膜早期阶段受影响的与MFRP相关的分子机制铺平道路,从而有可能将这些知识转化为确定晚期视网膜疾病所涉及机制的异同。