Mabry Alex, Kuzmicki Catherine E, O'Brien Angelina, Maggi Leonard B, Weber Jason D
Department of Medicine, Division of Molecular Oncology, Washington University School of Medicine, Saint Louis, Missouri, USA.
Cancer Biology Graduate Program, Washington University School of Medicine, Saint Louis, Missouri, USA.
Mol Cell Biol. 2025;45(6):246-261. doi: 10.1080/10985549.2025.2497817. Epub 2025 May 12.
The tumor suppressors p53 and ARF collaborate to prevent unwarranted cell proliferation and as such are two of the most frequently mutated genes in human cancer. Concomitant loss of functional p53 and ARF leads to massive gains in cell proliferation and transformation and is often observed in some of the most aggressive human cancer subtypes. These phenotypic gains are preceded by increased type I interferon (IFN) signaling that involves canonical STAT1 activation and a subsequent IFN-stimulated gene (ISG) signature. Here, we show that cells lacking p53 and ARF require active JAK1 to phosphorylate STAT1 on Y701 to maintain their high rate of proliferation. In fact, the use of selective JAK1 inhibitors ruxolitinib or baricitinib inhibited the induction of ISG's and the proliferation of p53 and ARF deleted cells. We identify a group of solid human tumors that lack functional p53 and ARF, show an expression signature of the upregulated type I IFN response genes, and are sensitive to selective JAK1 inhibitors. These data suggest that the type I IFN response acts as a positive driver of proliferation in the absence of p53 and ARF and, as such, presents itself as a potential therapeutic target in aggressive solid tumors.
肿瘤抑制因子p53和ARF协同作用以防止细胞过度增殖,因此是人类癌症中最常发生突变的两个基因。功能性p53和ARF的同时缺失会导致细胞增殖和转化大幅增加,这在一些最具侵袭性的人类癌症亚型中经常出现。这些表型变化之前会出现I型干扰素(IFN)信号增强,这涉及经典的STAT1激活以及随后的干扰素刺激基因(ISG)特征。在这里,我们表明缺乏p53和ARF的细胞需要活性JAK1将STAT1的Y701位点磷酸化,以维持其高增殖率。事实上,使用选择性JAK1抑制剂鲁索替尼或巴瑞替尼可抑制ISG的诱导以及p53和ARF缺失细胞的增殖。我们鉴定出一组缺乏功能性p53和ARF、表现出上调的I型干扰素反应基因表达特征且对选择性JAK1抑制剂敏感的实体人类肿瘤。这些数据表明,在缺乏p53和ARF的情况下,I型干扰素反应是增殖的正向驱动因素,因此是侵袭性实体肿瘤的潜在治疗靶点。