Xu Q, Tian J, Zhang J
Beijing Institute for Neurosciences, Capital University of Medical Sciences.
Zhonghua Wai Ke Za Zhi. 1997 Jan;35(1):5-9.
The rat model with a unilateral 6-OHDA-induced lesion of the dopaminergic system was used for experimental study on gene therapy for Parkinson's disease (PD). The plasmid pCMVTH (6.04 kb) was constructed as a vector containing the gene of tyrosine hydroxylase (TH) and transferred into cultured primary muscle cells by lipofection ex vivo. After expression of TH was determined in vitro, the intracerebral grafting (ICG) of these genetically modified cells was made in the striatum of PD rat model. The results showed that TH-expressing muscle cells had a long-term survival in the brain and induced a marked decrease in abnormal locomotion and increase in striatal dopamine levels for rat model.
采用单侧6-羟基多巴胺诱导的多巴胺能系统损伤大鼠模型进行帕金森病(PD)基因治疗的实验研究。构建了质粒pCMVTH(6.04 kb)作为载体,其含有酪氨酸羟化酶(TH)基因,并通过体外脂质转染法将其导入培养的原代肌肉细胞。在体外确定TH表达后,将这些基因修饰细胞脑内移植(ICG)到PD大鼠模型的纹状体中。结果显示,表达TH的肌肉细胞在脑内长期存活,并使大鼠模型的异常运动明显减少,纹状体多巴胺水平升高。