Candotti F
Disorders of Immunity Section, Clinical Gene Therapy Branch, National Human Genome Research Institute, National Institutes of Health, Bethesda, Maryland, USA.
Pediatr Clin North Am. 2000 Dec;47(6):1389-407. doi: 10.1016/s0031-3955(05)70277-7.
Several hurdles remain before gene therapy will be a part of mainstream medical therapy; however, the preliminary report of success in HSC correction in patients with XSCID provides hope that gene therapy will become a reality.