Wolańczyk T, Banaszkiewicz A, Mierzewska H, Czartoryska B, Zdziennicka E
Kliniki Psychiatrii Wieku Rozwojowego AM w Warszawie.
Psychiatr Pol. 2000 Sep-Oct;34(5):831-7.
Sanfilippo syndrome is one of mucopolysaccharidoses. The main symptom of this syndrome is regression of psychomotor development and neurological signs which occur between 2 and 6 years old. Unlike other mucopolysaccharidoses body dysmorfic features are relatively rare. Course of disease is progressive, most of the patients die before 20. The diagnosis is often difficult. In our opinion in each case presenting psychomotor regression of unknown origin metabolic disease should be excluded (e.g. urine analysis for mucopolysaccharides should be indicated). A 6 year old boy has been under psychiatric and psychological control since he was 3 due to psychomotor retardation, hyperactivity, autistic features, and behavioural disorder. In paediatric examination thickened facial features, coarse hair, knock-knees, short neck were noted. Genetic consultation set up the diagnosis of mucopolysaccharidosis type IIIA (Sanfilippo A disease).
桑菲利波综合征是黏多糖贮积症之一。该综合征的主要症状是精神运动发育迟缓和神经体征,这些症状出现在2至6岁之间。与其他黏多糖贮积症不同,身体畸形特征相对少见。疾病呈进行性发展,大多数患者在20岁前死亡。诊断往往很困难。我们认为,在每例出现不明原因精神运动发育迟缓的病例中,都应排除代谢性疾病(例如应进行尿黏多糖分析)。一名6岁男孩自3岁起就因精神运动发育迟缓、多动、自闭症特征和行为障碍接受精神科和心理科治疗。在儿科检查中,发现面部特征增厚、毛发粗糙、膝外翻、脖子短。基因咨询确诊为IIIA型黏多糖贮积症(桑菲利波A型疾病)。