Domènech Enric, Kruyer Helena, Gómez Carolina, Calvo Maria Teresa, Nunes Virginia
Centre de Genètica Mèdica i Molecular, Institut de Recerca Oncològica, L'Hospitalet de Llobregat, Barcelona, Spain.
Prenat Diagn. 2004 Oct;24(10):787-9. doi: 10.1002/pd.982.
Wolfram syndrome (WS) is an autosomal recessive neurodegenerative disorder characterized by early onset diabetes mellitus and progressive optic atrophy in the first decade of life. Other clinical features such as diabetes insipidus, deafness, renal tract abnormalities or psychiatric illnesses are often present. The sequence of the Wolfram syndrome gene (WFS1) was described in 1998, and mutations in the gene have been reported in many populations. To date, the function of the putative protein remains unknown. Here we report prenatal diagnosis by analysing the WFS1 gene, in a foetus belonging to a family with a child diagnosed for Wolfram syndrome. The parents are carriers of the c.2206G > C (G736R) mutation. To our knowledge this is the first description of prenatal diagnosis for Wolfram syndrome, based on the molecular analysis of the WFS1 gene.
沃夫勒姆综合征(WS)是一种常染色体隐性神经退行性疾病,其特征为在生命的第一个十年内出现早发性糖尿病和进行性视神经萎缩。通常还会出现其他临床特征,如尿崩症、耳聋、尿路异常或精神疾病。1998年描述了沃夫勒姆综合征基因(WFS1)的序列,并且在许多人群中都报告了该基因的突变。迄今为止,推定蛋白质的功能仍然未知。在此,我们报告了对一名胎儿进行产前诊断的情况,该胎儿来自一个有孩子被诊断为沃夫勒姆综合征的家庭。父母是c.2206G > C(G736R)突变的携带者。据我们所知,这是基于WFS1基因分子分析对沃夫勒姆综合征进行产前诊断的首次描述。