Majhail Navneet S, Weisdorf Daniel J, Defor Todd E, Miller Jeffrey S, McGlave Philip B, Slungaard Arne, Arora Mukta, Ramsay Norma K C, Orchard Paul J, MacMillan Margaret L, Burns Linda J
Blood and Marrow Transplant Program, Divisions of Medical and Pediatric Hematology, Oncology and Transplantation, University of Minnesota, Minneapolis, MN 55455, USA.
Biol Blood Marrow Transplant. 2006 Oct;12(10):1065-72. doi: 10.1016/j.bbmt.2006.06.006.
Autologous hematopoietic stem cell transplantation (ASCT) has become standard therapy for primary refractory (PR REF) or relapsed (REL) Hodgkin's lymphoma (HL); however, more than half of these patients eventually relapse and die of their disease. We studied long-term outcomes and evaluated factors influencing progression-free survival (PFS) in 141 patients with PR REF or REL HL who underwent ASCT between 1985 and 2003. Median age at ASCT was 30 years (range, 7-60 years); 21 patients had PR REF, and 120 had REL HL. With a median follow-up of 6.3 years (range, 1-20 years), the probability of PFS at 5 and 10 years was 48% (95% confidence interval [CI], 39%-57%) and 45% (95% CI, 36%-54%) and that of overall survival (OS) was 53% (95% CI, 44%-62%) and 47% (95% CI, 37%-57%), respectively. Transplant-related mortality at 100 days was 1.4%. Among 45 5- to 20-year survivors, no late relapses of HL were observed. In multivariate analysis, 3 factors were independently predictive of poor PFS: chemoresistant disease (relative risk [RR], 2.9; 95% CI, 1.7-5.0), B-symptoms at pretransplantation relapse (RR, 2.1; 95% CI, 1.3-3.4), and presence of residual disease at the time of transplantation (RR, 2.3; 95% CI, 1.1-4.8). Patients with 0 or 1 of these 3 adverse factors (low-risk disease) had a 5-year PFS of 67% (95% CI, 55%-79%) compared with 37% (95% CI, 22%-52%) in those with 2 factors (intermediate-risk group) and 9% (95% CI, 0-20%) in those with all 3 factors (high-risk group) (P < .001). The rates of OS at 5 years were 71% (95% CI, 60%-82%), 49% (95% CI, 33%-65%) and 13% (95% CI, 0-27%) in the 3 groups, respectively (P < .001). ASCT is associated with durable PFS in appropriately selected patients with PR REF or REL HL. Using a simple prognostic model, we can identify patients with high-risk disease who have predictably unfavorable outcome after ASCT and require novel therapeutic approaches. A risk-adapted approach should be followed in determining treatment options for patients with PR REF and REL HL.
自体造血干细胞移植(ASCT)已成为原发性难治性(PR REF)或复发性(REL)霍奇金淋巴瘤(HL)的标准治疗方法;然而,这些患者中超过一半最终会复发并死于该疾病。我们研究了1985年至2003年间接受ASCT的141例PR REF或REL HL患者的长期预后,并评估了影响无进展生存期(PFS)的因素。ASCT时的中位年龄为30岁(范围7 - 60岁);21例患者为PR REF,120例为REL HL。中位随访6.3年(范围1 - 20年),5年和10年时PFS的概率分别为48%(95%置信区间[CI],39% - 57%)和45%(95% CI,36% - 54%),总生存期(OS)的概率分别为53%(95% CI,44% - 62%)和47%(95% CI,37% - 57%)。100天时的移植相关死亡率为1.4%。在45例5至20年的幸存者中,未观察到HL的晚期复发。多因素分析中,3个因素独立预测PFS不良:化疗耐药性疾病(相对风险[RR],2.9;95% CI,1.7 - 5.0)、移植前复发时的B症状(RR,2.1;95% CI,1.3 - 3.4)以及移植时残留疾病的存在(RR,2.3;95% CI,1.1 - 4.8)。这3个不良因素中有0个或1个(低风险疾病)的患者5年PFS为67%(95% CI,55% - 79%),而有2个因素的患者(中风险组)为37%(95% CI,22% - 52%),有所有3个因素的患者(高风险组)为9%(95% CI,0 - 20%)(P <.001)。3组患者5年时的OS率分别为71%(95% CI,60% - 82%)、49%(95% CI,33% - 65%)和13%(95% CI,0 - 27%)(P <.001)。ASCT在适当选择的PR REF或REL HL患者中与持久的PFS相关。使用简单的预后模型,我们可以识别出ASCT后预后可预测不良且需要新治疗方法的高风险疾病患者。对于PR REF和REL HL患者,应采用风险适应性方法来确定治疗方案。