Shimohata Takayoshi, Hara Kenju, Sanpei Kazuhiro, Nunomura Jin-ichi, Maeda Tetsuya, Kawachi Izumi, Kanazawa Masato, Kasuga Kensaku, Miyashita Akinori, Kuwano Ryozo, Hirota Koichi, Tsuji Shoji, Onodera Osamu, Nishizawa Masatoyo, Honma Yoshiaki
Department of Neurology, Brain Research Institute, Niigata University, Niigata, Japan.
Brain. 2007 Sep;130(Pt 9):2302-9. doi: 10.1093/brain/awm036. Epub 2007 Apr 2.
Autosomal dominant choreas are genetically heterogeneous disorders including Huntington disease (HD), Huntington disease like 1 (HDL1), Huntington disease like 2 (HDL2), dentatorubro-pallidoluysian atrophy (DRPLA), spinocerebellar ataxia type 17 (SCA17) and benign hereditary chorea (BHC). We identified two Japanese families with adult-onset benign chorea without dementia inherited in an autosomal dominant pattern. All affected individuals presented slowly progressive choreic movements in their upper and lower extremities, trunk and head with an age of onset ranging from 40 to 66 (average 54.3), which were markedly improved by haloperidol. The affected individuals also developed reduced muscle tones in their extremities. The findings obtained in the brain CT or MRI studies of nine affected individuals were normal. These clinical features resemble those of the so-called 'senile chorea'. HD, HDL1, HDL2, DRPLA, SCA17 and BHC caused by mutations in the TITF-1 gene were excluded by mutational and linkage analyses. A genome-wide linkage analysis revealed linkage to chromosome 8q21.3-q23.3 with a maximum cumulative two-point log of the odds (LOD) score of 4.74 at D8S1784 (theta = 0.00). Haplotype analysis of both the families defined the candidate region as 21.5 Mb interval flanked by M9267 and D8S1139. We named this adult-onset dominant inherited chorea 'benign hereditary chorea type 2 (BHC2)'.
常染色体显性遗传性舞蹈病是一类具有遗传异质性的疾病,包括亨廷顿舞蹈病(HD)、亨廷顿舞蹈病样1型(HDL1)、亨廷顿舞蹈病样2型(HDL2)、齿状核红核苍白球路易体萎缩症(DRPLA)、脊髓小脑共济失调17型(SCA17)和良性遗传性舞蹈病(BHC)。我们鉴定了两个日本家族,其成年发病的良性舞蹈病呈常染色体显性模式遗传且无痴呆症状。所有受累个体均表现为上肢、下肢、躯干和头部缓慢进展的舞蹈样动作,发病年龄在40至66岁之间(平均54.3岁),氟哌啶醇可使其明显改善。受累个体还出现四肢肌张力降低。对9名受累个体进行的脑部CT或MRI研究结果均正常。这些临床特征类似于所谓的“老年性舞蹈病”。通过突变和连锁分析排除了由TITF-1基因突变引起的HD、HDL1、HDL2、DRPLA、SCA17和BHC。全基因组连锁分析显示与8号染色体q21.3-q23.3区域连锁,在D8S1784位点最大累积两点对数优势(LOD)得分为4.74(θ = 0.00)。对两个家族进行单倍型分析,将候选区域确定为M9267和D8S1139之间的21.5 Mb区间。我们将这种成年发病的显性遗传性舞蹈病命名为“良性遗传性舞蹈病2型(BHC2)”。