Steinberg M H
Veterans Affairs Medical Center, Jackson, MS 39216.
Am J Med Sci. 1991 Nov;302(5):298-303. doi: 10.1097/00000441-199111000-00008.
Gene therapy offers the promise of a definitive cure of the hemoglobinopathies and thalassemias. The background of gene therapy for these disorders is discussed along with the obstacles that must be overcome before this promise becomes reality.
基因治疗有望彻底治愈血红蛋白病和地中海贫血。本文讨论了针对这些疾病的基因治疗背景以及在这一前景成为现实之前必须克服的障碍。