Wijburg M T, Wenniger-Prick L J Maillette de Buy, Bosch A M, Visser G, Bams-Mengerink A
Universitair Medisch Centrum Utrecht, divisie Kinderen, Huispost KC 03.063.0, Lundlaan 6, 3584 EA Utrecht.
Ned Tijdschr Geneeskd. 2008 Mar 15;152(11):632-6.
In three young patients who presented with bilateral cataracts the cause proved to be an inherited metabolic disease. The first patient was a newborn aged 7 weeks, in whom galactokinase deficiency was diagnosed. The second patient was a boy aged 8 years with cerebrotendinous xanthomatosis. The third patient was a girl who was diagnosed with cataracts at the age of 3 months. At the age of 4 years the diagnosis 'rhizomelic chondrodysplasia punctata' was established. Screening for metabolic disorders in all children with bilateral cataracts is essential, as in some disorders progressive and severe symptoms can be avoided with timely initiation of treatment. In addition, diagnosis allows for family studies and genetic counselling to take place. This may result in prevention of disease by early therapeutic intervention and prenatal screening.
在三名出现双侧白内障的年轻患者中,病因被证明是一种遗传性代谢疾病。第一名患者是一名7周大的新生儿,被诊断出患有半乳糖激酶缺乏症。第二名患者是一名8岁男孩,患有脑腱性黄瘤病。第三名患者是一名女孩,3个月大时被诊断出患有白内障。4岁时确诊为“肢根型点状软骨发育不良”。对所有双侧白内障患儿进行代谢紊乱筛查至关重要,因为在某些疾病中,及时开始治疗可以避免进行性和严重症状的出现。此外,诊断有助于进行家族研究和遗传咨询。这可能通过早期治疗干预和产前筛查来预防疾病。