MRC Mammalian Genetics Unit, Harwell, OX11 0RD, UK.
Genes Brain Behav. 2009 Oct;8(7):699-713. doi: 10.1111/j.1601-183X.2009.00514.x. Epub 2009 Jun 22.
Deafness is the most common sensory disorder in humans and the aetiology of genetic deafness is complex. Mouse mutants have been crucial in identifying genes involved in hearing. However, many deafness genes remain unidentified. Using N-ethyl N-nitrosourea (ENU) mutagenesis to generate new mouse models of deafness, we identified a novel semi-dominant mouse mutant, Cloth-ears (Clth). Cloth-ears mice show reduced acoustic startle response and mild hearing loss from approximately 30 days old. Auditory-evoked brainstem response (ABR) and distortion product otoacoustic emission (DPOAE) analyses indicate that the peripheral neural auditory pathway is impaired in Cloth-ears mice, but that cochlear function is normal. In addition, both Clth/Clth and Clth/+ mice display paroxysmal tremor episodes with behavioural arrest. Clth/Clth mice also show a milder continuous tremor during movement and rest. Longitudinal phenotypic analysis showed that Clth/+ and Clth/Clth mice also have complex defects in behaviour, growth, neurological and motor function. Positional cloning of Cloth-ears identified a point mutation in the neuronal voltage-gated sodium channel alpha-subunit gene, Scn8a, causing an aspartic acid to valine (D981V) change six amino acids downstream of the sixth transmembrane segment of the second domain (D2S6). Complementation testing with a known Scn8a mouse mutant confirmed that this mutation is responsible for the Cloth-ears phenotype. Our findings suggest a novel role for Scn8a in peripheral neural hearing loss and paroxysmal motor dysfunction.
耳聋是人类最常见的感觉障碍,遗传性耳聋的病因复杂。鼠突变体在鉴定参与听力的基因方面发挥了重要作用。然而,许多耳聋基因仍未被识别。我们使用 N-乙基-N-亚硝基脲(ENU)诱变剂生成新的耳聋小鼠模型,发现了一种新型的半显性小鼠突变体,Cloth-ears(Clth)。Clth 小鼠表现出对声音的惊跳反应降低和大约 30 天龄时出现轻度听力损失。听觉脑干反应(ABR)和畸变产物耳声发射(DPOAE)分析表明,Clth 小鼠的外周神经听觉通路受损,但耳蜗功能正常。此外,Clth/Clth 和 Clth/+ 小鼠都表现出阵发性震颤发作和行为停止。Clth/Clth 小鼠在运动和休息时还表现出轻微的持续震颤。纵向表型分析表明,Clth/+ 和 Clth/Clth 小鼠在行为、生长、神经和运动功能方面也存在复杂缺陷。Cloth-ears 的定位克隆确定了神经元电压门控钠通道 alpha 亚基基因 Scn8a 的一个点突变,导致第六跨膜区第二域(D2S6)下游第六个氨基酸残基的天冬氨酸突变为缬氨酸(D981V)。与已知的 Scn8a 小鼠突变体的互补性测试证实,该突变是导致 Clth 表型的原因。我们的研究结果表明 Scn8a 在周围神经听力损失和阵发性运动功能障碍中具有新的作用。