Department of Clinical Genetics, University Hospitals Bristol NHS Foundation Trust, Bristol, UK.
Am J Med Genet A. 2009 Dec;149A(12):2838-42. doi: 10.1002/ajmg.a.33124.
In 1985, Mardini and Nyhan described three patients from consanguineous families with unilateral complete/partial lung agenesis, congenital cardiac defects, and ipsilateral thumb anomalies. Although there have been many reports of lung agenesis with other malformations, especially hemifacial microsomia and radial ray anomalies, very few demonstrate this triad of defects. We describe three patients with the Mardini-Nyhan association which may represent a distinct entity, although this remains uncertain at present. A fourth patient is also described, the sister of one of the other patients, with complex congenital cardiac disease and bilateral lung lobation abnormalities. This is the first reported incidence of a possible recurrence within a family and suggests, together with the consanguinity observed by Mardini and Nyhan, that recessive inheritance should be considered in genetic counseling for this disorder.
1985 年,Mardini 和 Nyhan 描述了来自近亲家庭的 3 名患者,他们均患有单侧完全/部分肺发育不全、先天性心脏缺陷和同侧拇指畸形。尽管有许多关于肺部发育不全伴其他畸形的报道,尤其是单侧颜面短小和桡侧射线异常,但很少有报道显示这三种缺陷同时存在。我们描述了 3 名患有 Mardini-Nyhan 综合征的患者,尽管目前这可能代表一种独特的实体,但仍不确定。还描述了第 4 名患者,是其中 1 名患者的妹妹,患有复杂的先天性心脏病和双侧肺叶异常。这是首次报道在一个家族中可能出现的复发情况,这与 Mardini 和 Nyhan 观察到的近亲结婚一起表明,在这种疾病的遗传咨询中应考虑隐性遗传。