Washington State University College of Veterinary Medicine, Pullman, USA.
Hum Genet. 2010 Sep;128(3):315-24. doi: 10.1007/s00439-010-0855-y. Epub 2010 Jul 2.
Arrhythmogenic right ventricular cardiomyopathy (ARVC) is a familial cardiac disease characterized by ventricular arrhythmias and sudden cardiac death. It is most frequently inherited as an autosomal dominant trait with incomplete and age-related penetrance and variable clinical expression. The human disease is most commonly associated with a causative mutation in one of several genes encoding desmosomal proteins. We have previously described a spontaneous canine model of ARVC in the boxer dog. We phenotyped adult boxer dogs for ARVC by performing physical examination, echocardiogram and ambulatory electrocardiogram. Genome-wide association using the canine 50k SNP array identified several regions of association, of which the strongest resided on chromosome 17. Fine mapping and direct DNA sequencing identified an 8-bp deletion in the 3' untranslated region (UTR) of the Striatin gene on chromosome 17 in association with ARVC in the boxer dog. Evaluation of the secondary structure of the 3' UTR demonstrated that the deletion affects a stem loop structure of the mRNA and expression analysis identified a reduction in Striatin mRNA. Dogs that were homozygous for the deletion had a more severe form of disease based on a significantly higher number of ventricular premature complexes. Immunofluorescence studies localized Striatin to the intercalated disc region of the cardiac myocyte and co-localized it to three desmosomal proteins, Plakophilin-2, Plakoglobin and Desmoplakin, all involved in the pathogenesis of ARVC in human beings. We suggest that Striatin may serve as a novel candidate gene for human ARVC.
致心律失常性右室心肌病(ARVC)是一种家族性心脏病,其特征为室性心律失常和心脏性猝死。它最常以不完全且与年龄相关的外显率和可变的临床表现遗传为常染色体显性遗传。人类疾病最常与几个编码桥粒蛋白的基因之一的致病突变相关。我们之前曾在拳师犬中描述过 ARVC 的自发性犬模型。我们通过体格检查、超声心动图和动态心电图对成年拳师犬进行 ARVC 表型分析。使用犬 50k SNP 芯片进行全基因组关联分析确定了几个关联区域,其中最强的区域位于第 17 号染色体上。精细映射和直接 DNA 测序确定了第 17 号染色体上 Striatin 基因 3'非翻译区(UTR)的 8 个碱基对缺失与拳师犬 ARVC 相关。对 3'UTR 的二级结构的评估表明,该缺失影响了 mRNA 的茎环结构,表达分析确定 Striatin mRNA 减少。携带该缺失的犬由于室性早搏数量显著增加,表现出更严重的疾病形式。免疫荧光研究将 Striatin 定位在心脏肌细胞的闰盘区域,并与三种桥粒蛋白(桥粒斑蛋白-2、桥粒结合蛋白和桥粒芯胶蛋白)共定位,这些蛋白均参与人类 ARVC 的发病机制。我们认为 Striatin 可能是人类 ARVC 的一个新候选基因。