Department of Pediatric Endocrinology, Mater Children's Hospital, South Brisbane, Queensland 4101, Australia.
J Clin Endocrinol Metab. 2010 Dec;95(12):E464-7. doi: 10.1210/jc.2010-0647. Epub 2010 Sep 1.
It has been postulated that central adrenal insufficiency (CAI), resulting from hypothalamic dysfunction, may contribute to the increased unexplained death rates in Prader Willi syndrome (PWS). A study using the overnight metyrapone test reported a 60% prevalence of CAI in children with PWS. We used a low-dose Synacthen test to screen for CAI in children with PWS.
We studied 41 children with genetic diagnosis of PWS [20 males; mean age, 7.68 (±5.23) yr] in five pediatric endocrinology centers in Australasia. All participants were randomly selected, and none had a history of Addisonian crisis. Ten of the cohort were receiving sex hormone therapy, 19 were receiving GH, and four were receiving T4. Their mean body mass index z-score was +1.48 (±1.68). Baseline morning ACTH and cortisol levels were measured, followed by iv administration of 1 μg Synacthen. Post-Synacthen cortisol levels were measured at 30 min, and a cortisol level above 500 nmol/liter was considered normal.
The mean baseline ACTH and cortisol were 15 (±14) ng/liter and 223 (±116) nmol/liter, respectively. The mean 30-min plasma cortisol was 690 (±114) nmol/liter, and the average increase from baseline was 201%.
Our result suggests that CAI is rare in children with PWS.
据推测,由于下丘脑功能障碍导致的中枢性肾上腺功能不全(CAI)可能导致 Prader-Willi 综合征(PWS)中未明原因的死亡率增加。一项使用 overnight metyrapone 试验的研究报告称,PWS 儿童中 CAI 的患病率为 60%。我们使用低剂量 Synacthen 试验筛查 PWS 儿童的 CAI。
我们在澳大利亚的五个儿科内分泌中心研究了 41 名具有 PWS 遗传诊断的儿童[20 名男性;平均年龄 7.68(±5.23)岁]。所有参与者均为随机选择,且均无 Addisonian 危机病史。该队列中有 10 名正在接受性激素治疗,19 名正在接受 GH 治疗,4 名正在接受 T4 治疗。他们的平均体重指数 z 分数为+1.48(±1.68)。测量了清晨 ACTH 和皮质醇基础水平,随后静脉内给予 1 μg Synacthen。测量 Synacthen 后 30 分钟的皮质醇水平,皮质醇水平高于 500 nmol/l 被认为正常。
平均基线 ACTH 和皮质醇分别为 15(±14)ng/l 和 223(±116)nmol/l。30 分钟时平均血浆皮质醇为 690(±114)nmol/l,平均基线增加 201%。
我们的结果表明,PWS 儿童中 CAI 罕见。