Department of Clinical Genetics, Erasmus Medical Center, Rotterdam, The Netherlands.
Am J Med Genet A. 2012 Oct;158A(10):2412-20. doi: 10.1002/ajmg.a.35517. Epub 2012 Aug 14.
Interstitial deletions of the chromosome 22q11.2 region are the most common microdeletions in humans. The TBX1 gene is considered to be the major candidate gene for the main features in 22q11.2 deletion syndrome, including congenital heart malformations, (para)thyroid hypoplasia, and craniofacial abnormalities. We report on eight patients with atypical deletions of chromosome 22q11.2. These deletions comprise the distal part of the common 22q11.2 deleted region but do not encompass the TBX1 gene. Ten similar patients with overlapping distal 22q11.2 deletions have been reported previously. The clinical features of these patients are described and compared to those found in the classic 22q11.2 deletion syndrome. We discuss the possible roles of a position effect or haploinsufficiency of distally located genes (e.g., CRKL) in the molecular pathogenesis of the 22q11.2 deletion syndrome.
染色体 22q11.2 区域的染色质间缺失是人类中最常见的微缺失之一。TBX1 基因被认为是 22q11.2 缺失综合征主要特征的主要候选基因,这些特征包括先天性心脏畸形、(副)甲状腺发育不全和颅面异常。我们报告了 8 例染色体 22q11.2 非典型缺失的患者。这些缺失包括常见的 22q11.2 缺失区域的远端部分,但不包括 TBX1 基因。以前曾报道过 10 例具有重叠的远端 22q11.2 缺失的相似患者。描述了这些患者的临床特征,并与经典的 22q11.2 缺失综合征进行了比较。我们讨论了远端基因(如 CRKL)的位置效应或杂合性不足在 22q11.2 缺失综合征分子发病机制中的可能作用。