Center for Thrombosis and Hemostasis, Professor-Hess-Kinderklinik, Klinikum Bremen-Mitte, Bremen, Germany.
Haemophilia. 2013 May;19(3):438-44. doi: 10.1111/hae.12075. Epub 2012 Dec 20.
Inhibitor development against von Willebrand factor, factor VIII or factor IX is one of the most severe complications of treating patients with von Willebrand's disease (VWD), haemophilia A or haemophilia B respectively. Continuous infusion of factor concentrate has been implicated as a risk factor for inhibitor development. This prospective study investigated inhibitor development after continuous infusion of factor concentrate for surgical procedures in subjects with VWD or a severe form of haemophilia (factor activity <1%). Observations were made on the occurrence of inhibitor formation, adverse events and virus seroconversions. Main inclusion criteria comprised a negative history of inhibitors to replacement factor concentrate, ≥ 50 exposure days to factor concentrate and anticipated surgery requiring replacement factor coverage for ≥ 3 days. Therapy began with a bolus dose of 30-50 IU kg(-1) body weight of factor concentrate followed by continuous infusion with 3-4 IU kg(-1) h(-1) . Continuous infusion dose of factor concentrate was adjusted based on factor levels measured at least once daily. In 46 subjects included in the study to date, no inhibitors have been identified at discharge or follow-up (3-4 weeks after surgery), and no thrombotic events or postoperative wound infections occurred. All subjects underwent surgery without major blood loss, and hemostatic efficacy was generally rated 'excellent'. The results of the current study are promising, although the number of subjects is too small to make a definitive statement about the incidence of inhibitor development during continuous infusion of factor concentrate. Therefore, this study will be continued.
针对血管性血友病因子 (VWF)、VIII 因子或 IX 因子的抑制剂开发是分别治疗血管性血友病 (VWD)、A型血友病或 B 型血友病患者的最严重并发症之一。连续输注因子浓缩物已被认为是抑制剂发展的一个危险因素。这项前瞻性研究调查了 VWD 或严重形式血友病(因子活性 <1%)患者在手术中连续输注因子浓缩物后抑制剂的发展情况。观察抑制剂形成、不良事件和病毒血清转换的发生情况。主要纳入标准包括:无替代因子浓缩物抑制剂的病史、≥50 天暴露于因子浓缩物和预计手术需要≥3 天的替代因子覆盖。治疗开始时给予 30-50IU/kg 体重的因子浓缩物冲击剂量,然后以 3-4IU/kg/h 的速度持续输注。根据每天至少测量一次的因子水平调整连续输注的因子浓缩物剂量。在迄今为止纳入研究的 46 名受试者中,出院或随访时(手术 3-4 周后)未发现抑制剂,也未发生血栓事件或术后伤口感染。所有受试者均在无大量失血的情况下接受了手术,止血效果通常被评为“优秀”。尽管目前研究的受试者数量太少,无法对连续输注因子浓缩物期间抑制剂发展的发生率做出明确的结论,但当前研究的结果是有希望的。因此,这项研究将继续进行。