Kober Daniel L, Wanhainen Kelsey M, Johnson Britney M, Randolph David T, Holtzman Michael J, Brett Tom J
Molecular Microbiology and Microbial Pathogenesis Program, Washington University School of Medicine, St. Louis, MO 63110, United States; Department of Internal Medicine, Washington University School of Medicine, St. Louis, MO 63110, United States.
Department of Internal Medicine, Washington University School of Medicine, St. Louis, MO 63110, United States.
Protein Expr Purif. 2014 Apr;96:32-8. doi: 10.1016/j.pep.2014.01.015. Epub 2014 Feb 7.
TREM-2 (triggering receptor expressed on myeloid cells-2) is an innate immune receptor expressed on dendritic cells, macrophages, osteoclasts, and microglia. Recent genetic studies have reported the occurrence of point mutations in TREM-2 that correlate with a dramatically increased risk for the development of neurodegenerative diseases, including Alzheimer's disease, frontotemporal dementia, and Parkinson's disease. Structural and biophysical studies of wild-type and mutant TREM-2 ectodomains are required to understand the functional consequences of these mutations. In order to facilitate these studies, we undertook the production and crystallization of these proteins. Here we demonstrate that, unlike many single Ig domain proteins, TREM-2 could not be readily refolded from bacterially-expressed inclusion bodies. Instead, we developed a mammalian-cell based expression system for the successful production of wild-type and mutant TREM-2 proteins in milligram quantities and a single-chromatography-step purification scheme that produced diffraction-quality crystals. These crystals diffract to a resolution of 3.3 Å and produce data sufficient for structure determination. We describe herein the procedures to produce wild-type and mutant human TREM-2 Ig domains in sufficient quantities for structural and biophysical studies. Such studies are crucial to understand the functional consequences of TREM-2 point mutations linked to the development of neurodegenerative diseases and, ultimately, to develop patient-specific molecular therapies to treat them.
触发受体表达于髓样细胞-2(TREM-2)是一种在树突状细胞、巨噬细胞、破骨细胞和小胶质细胞上表达的固有免疫受体。最近的遗传学研究报道,TREM-2中发生的点突变与神经退行性疾病(包括阿尔茨海默病、额颞叶痴呆和帕金森病)发展风险的显著增加相关。需要对野生型和突变型TREM-2胞外域进行结构和生物物理研究,以了解这些突变的功能后果。为了促进这些研究,我们开展了这些蛋白质的生产和结晶工作。在此我们证明,与许多单Ig结构域蛋白不同,TREM-2不能轻易地从细菌表达的包涵体中重折叠。相反,我们开发了一种基于哺乳动物细胞的表达系统,成功地以毫克量生产野生型和突变型TREM-2蛋白,并开发了一种单步色谱纯化方案,该方案产生了适合衍射的晶体。这些晶体的衍射分辨率为3.3 Å,并产生了足以进行结构测定的数据。我们在此描述了生产足够量野生型和突变型人TREM-2 Ig结构域以用于结构和生物物理研究的方法。此类研究对于理解与神经退行性疾病发展相关的TREM-2点突变的功能后果至关重要,最终对于开发针对患者的分子疗法来治疗这些疾病也至关重要。