Department of Chemistry and Chemical Biology, Northeastern University , Boston, Massachusetts 02115, United States.
J Med Chem. 2014 Jun 12;57(11):4834-48. doi: 10.1021/jm500361r. Epub 2014 May 21.
Compound NVP-BEZ235 (1) is a potent inhibitor of human phospoinositide-3-kinases and mammalian target of rapamycin (mTOR) that also showed high inhibitory potency against Trypanosoma brucei cultures. With an eye toward using 1 as a starting point for anti-trypanosomal drug discovery, we report efforts to reduce host cell toxicity, to improve the physicochemical properties, and to improve the selectivity profile over human kinases. In this work, we have developed structure-activity relationships for analogues of 1 and have prepared analogues of 1 with improved solubility properties and good predicted central nervous system exposure. In this way, we have identified 4e, 9, 16e, and 16g as the most promising leads to date. We also report cell phenotype and phospholipidomic studies that suggest that these compounds exert their anti-trypanosomal effects, at least in part, by inhibition of lipid kinases.
化合物 NVP-BEZ235(1)是一种有效的人磷酸肌醇-3-激酶和雷帕霉素靶蛋白(mTOR)抑制剂,对布鲁氏锥虫培养物也显示出很高的抑制活性。为了将 1 用作抗锥虫药物发现的起点,我们致力于降低宿主细胞毒性,改善物理化学性质,并提高对人激酶的选择性。在这项工作中,我们已经开发出了 1 的类似物的构效关系,并制备了具有改善的溶解性和良好的中枢神经系统暴露预测的 1 的类似物。通过这种方式,我们确定了 4e、9、16e 和 16g 是迄今为止最有前途的先导化合物。我们还报告了细胞表型和磷脂组学研究,表明这些化合物通过抑制脂质激酶发挥其抗锥虫作用,至少部分如此。