European Medicines Agency review of ataluren for the treatment of ambulant patients aged 5 years and older with Duchenne muscular dystrophy resulting from a nonsense mutation in the dystrophin gene.
作者信息
Haas Manuel, Vlcek Viktor, Balabanov Pavel, Salmonson Tomas, Bakchine Serge, Markey Greg, Weise Martina, Schlosser-Weber Gabriele, Brohmann Henning, Yerro Concepcion Prieto, Mendizabal Macarena Rodriguez, Stoyanova-Beninska Violeta, Hillege Hans L
机构信息
European Medicines Agency, London, United Kingdom.
European Medicines Agency, London, United Kingdom.
出版信息
Neuromuscul Disord. 2015 Jan;25(1):5-13. doi: 10.1016/j.nmd.2014.11.011. Epub 2014 Nov 24.
PMID:25497400
Abstract
摘要
Zotero 插件