Chen Hong-Jung, Chen Chien-Hsi, Chang Ming-Yao, Tsai Da-Ching, Baum Ellen Z, Hariri Robert, Herzberg Uri, Hsieh Patrick C H
Celgene Cellular Therapeutics, Warren, New Jersey, USA; Institute of Clinical Medicine, National Cheng Kung University, Tainan, Taiwan, Republic of China; Institute of Biomedical Sciences, Academia Sinica, Taipei, Taiwan, Republic of China.
Celgene Cellular Therapeutics, Warren, New Jersey, USA; Institute of Clinical Medicine, National Cheng Kung University, Tainan, Taiwan, Republic of China; Institute of Biomedical Sciences, Academia Sinica, Taipei, Taiwan, Republic of China
Stem Cells Transl Med. 2015 Mar;4(3):269-75. doi: 10.5966/sctm.2014-0135. Epub 2015 Feb 11.
Human placenta-derived adherent cells (PDACs) are a culture-expanded, undifferentiated mesenchymal-like population derived from full-term placental tissue, with immunomodulatory, anti-inflammatory, angiogenic, and neuroprotective properties. PDA-001 (cenplacel-L), an intravenous formulation of PDAC cells, is in clinical development for the treatment of autoimmune and inflammatory diseases. We tested the therapeutic effects of PDA-001 in mice with chronic heart failure (CHF). Three weeks after transaortic constriction surgery to induce CHF, the mice underwent direct intramyocardial (IM) or i.v. injection of PDA-001 at a high (0.5 × 10(6) cells per mouse), medium (0.5 × 10(5) cells per mouse), or low (0.5 × 10(4) cells per mouse) dose. The mice were sacrificed 4 weeks after treatment. Echocardiography and ventricular catheterization showed that IM injection of PDA-001 significantly improved left ventricular systolic and diastolic function compared with injection of vehicle or i.v. injection of PDA-001. IM injection of PDA-001 also decreased cardiac fibrosis, shown by trichrome staining in the vicinity of the injection sites. Low-dose treatment showed the best improvement in cardiac performance compared with the medium- and high-dose groups. In another independent study to determine the mechanism of action with bromodeoxyuridine labeling, the proliferation rates of endothelial cells and cardiomyocytes were significantly increased by low or medium IM dose PDA-001. However, no surviving PDA-001 cells were detected in the heart 1 month after injection. In vivo real-time imaging consistently revealed that the PDA-001 cells were detectable only within 2 days after IM injection of luciferase-expressing PDA-001. Together, these results have demonstrated the cardiac therapeutic potential of PDA-001, likely through a paracrine effect.
人胎盘来源的贴壁细胞(PDACs)是一种经培养扩增的、未分化的间充质样细胞群体,源自足月胎盘组织,具有免疫调节、抗炎、血管生成和神经保护特性。PDA - 001(cenplacel - L)是一种PDAC细胞的静脉制剂,正在进行治疗自身免疫性和炎性疾病的临床开发。我们在慢性心力衰竭(CHF)小鼠中测试了PDA - 001的治疗效果。在进行经主动脉缩窄手术诱导CHF三周后,小鼠接受高剂量(每只小鼠0.5×10⁶个细胞)、中剂量(每只小鼠0.5×10⁵个细胞)或低剂量(每只小鼠0.5×10⁴个细胞)的PDA - 001直接心肌内(IM)或静脉注射。治疗4周后处死小鼠。超声心动图和心室导管检查显示,与注射赋形剂或静脉注射PDA - 001相比,心肌内注射PDA - 001显著改善了左心室收缩和舒张功能。心肌内注射PDA - 001还减少了心脏纤维化,注射部位附近的三色染色显示了这一点。与中剂量和高剂量组相比,低剂量治疗对心脏功能的改善最佳。在另一项使用溴脱氧尿苷标记来确定作用机制的独立研究中,低剂量或中剂量心肌内注射PDA - 001可显著提高内皮细胞和心肌细胞的增殖率。然而,注射后1个月在心脏中未检测到存活的PDA - 001细胞。体内实时成像一致显示,仅在注射表达荧光素酶的PDA - 001后2天内可检测到PDA - 001细胞。总之,这些结果证明了PDA - 001的心脏治疗潜力,可能是通过旁分泌作用实现的。