Hao Shuyu, Hong Christopher S, Feng Jie, Yang Chunzhang, Chittiboina Prashant, Zhang Junting, Zhuang Zhengping
Department of Neurological Surgery, Beijing Tiantan Hospital;
National Institute of Neurological Disorders and Stroke, Surgical Neurology Branch, National Institutes of Health, Bethesda, Maryland.
J Neurosurg. 2016 Jun;124(6):1562-7. doi: 10.3171/2015.4.JNS15191. Epub 2015 Oct 16.
Maffucci syndrome is a rare disease characterized by multiple enchondromas and soft-tissue hemangiomas. Additionally, neuroendocrine tumors including pituitary adenomas have been described in these patients. The underlying genetic etiology lies in somatic mosaicism of mutations in isocitrate dehydrogenase 1 (IDH1) or isocitrate dehydrogenase 2 (IDH2). This report describes a patient with Maffucci syndrome who presented with intracranial tumors of the skull base and suprasellar region. The patient underwent resection of both intracranial tumors, revealing histopathological diagnoses of chondrosarcoma and pituitary adenoma. DNA sequencing of the tumors was performed to identify common IDH1/2 mutations. Clinical, radiological, and biochemical assessments were performed. Genotypic studies used standard Sanger sequencing in conjunction with a target-specific peptide nucleic acid to detect IDH1 mutations in tumor tissues. DNA sequencing demonstrated identical IDH1 mutations (c.394C > T) in both tumors. To the authors' knowledge, this report provides the first genetic evidence for the inclusion of pituitary adenomas among tumors characterizing Maffucci syndrome. In patients who are newly diagnosed with Maffucci syndrome, it is appropriate to monitor for development of pituitary pathology and neuroendocrine dysfunction.
马富西综合征是一种罕见疾病,其特征为多发性内生软骨瘤和软组织血管瘤。此外,这些患者中还曾有包括垂体腺瘤在内的神经内分泌肿瘤的报道。潜在的遗传病因在于异柠檬酸脱氢酶1(IDH1)或异柠檬酸脱氢酶2(IDH2)突变的体细胞镶嵌现象。本报告描述了一名患有马富西综合征的患者,该患者出现了颅底和鞍上区域的颅内肿瘤。患者接受了颅内肿瘤的切除手术,术后组织病理学诊断为软骨肉瘤和垂体腺瘤。对肿瘤进行了DNA测序以确定常见的IDH1/2突变。进行了临床、放射学和生化评估。基因分型研究采用标准桑格测序法结合靶向特异性肽核酸来检测肿瘤组织中的IDH1突变。DNA测序显示两个肿瘤中均存在相同的IDH1突变(c.394C>T)。据作者所知,本报告首次提供了遗传学证据,表明垂体腺瘤属于马富西综合征特征性肿瘤。对于新诊断为马富西综合征的患者,监测垂体病变和神经内分泌功能障碍的发生情况是合适的。