Soverini Simona, De Benedittis Caterina, Mancini Manuela, Martinelli Giovanni
Department of Experimental, Diagnostic and Specialty Medicine, Haematology/Oncology "L. e A. Seràgnoli", University of Bologna, Bologna, Italy.
Br J Haematol. 2016 May;173(3):337-49. doi: 10.1111/bjh.13966. Epub 2016 Mar 7.
Currently, physicians treating chronic myeloid leukaemia (CML) patients can rely on a wide spectrum of therapeutic options: the best use of such options is essential to achieve excellent clinical outcomes and, possibly, treatment-free remission (TFR). To accomplish this, proper integration of expert clinical and laboratory monitoring of CML patients is fundamental. Molecular response (MR) monitoring of patients at defined time points has emerged as an important success factor for optimal disease management and BCR-ABL1 kinase domain mutation screening is useful to guide therapeutic reassessment in patients who do not achieve optimal responses to tyrosine kinase inhibitor therapy. Deeper MRs might be associated with improved long-term survival outcomes. More importantly, they are considered a gateway to TFR. In molecular biology, novel procedures and technologies are continually being developed. More sophisticated molecular tools and automated analytical solutions are emerging as CML treatment endpoints and expectations become more and more ambitious. Here we provide a critical overview of current and novel methodologies, present their strengths and pitfalls and discuss what their present and future role might be.
目前,治疗慢性髓性白血病(CML)患者的医生可以依赖多种治疗选择:充分利用这些选择对于实现优异的临床结果以及可能的无治疗缓解(TFR)至关重要。要做到这一点,对CML患者进行专业的临床和实验室监测的适当整合是至关重要的。在特定时间点对患者进行分子反应(MR)监测已成为优化疾病管理的重要成功因素,而BCR-ABL1激酶结构域突变筛查有助于指导对酪氨酸激酶抑制剂治疗未达到最佳反应的患者进行治疗重新评估。更深层次的MR可能与改善长期生存结果相关。更重要的是,它们被认为是通向TFR的途径。在分子生物学领域,新的程序和技术不断涌现。随着CML治疗终点和期望变得越来越高,更精密的分子工具和自动化分析解决方案正在出现。在此,我们对当前和新出现的方法进行批判性概述,介绍它们的优点和缺陷,并讨论它们目前和未来可能发挥的作用。