Nicotra Alessia, Newman Claus, Johnson Martin, Eremin Oleg, Friede Tim, Malik Omar, Nicholas Richard
Department of Neurosciences, Imperial College Healthcare NHS Trust, Charing Cross Hospital, Fulham Palace Road, London, W6 8RF, United Kingdom.
Thalidomide Trust, 1 Eaton Court Road, Colmworth Business Park, Eaton Socon, St Neots, Cambridgeshire, PE19 8ER, United Kingdom.
PLoS One. 2016 Apr 21;11(4):e0152902. doi: 10.1371/journal.pone.0152902. eCollection 2016.
Phocomelia is an extremely rare congenital malformation that emerged as one extreme of a range of defects resulting from in utero exposure to thalidomide. Individuals with thalidomide embryopathy (TE) have reported developing symptoms suggestive of peripheral nervous system dysfunction in the mal-developed limbs in later life.
Case control study comparing TE subjects with upper limb anomalies and neuropathic symptoms with healthy controls using standard neurophysiological testing. Other causes of a peripheral neuropathy were excluded prior to assessment.
Clinical examination of 17 subjects with TE (aged 50.4±1.3 [mean±standard deviation] years, 10 females) and 17 controls (37.9±9.0 years; 8 females) demonstrated features of upper limb compressive neuropathy in three-quarters of subjects. Additionally there were examination findings suggestive of mild sensory neuropathy in the lower limbs (n = 1), L5 radiculopathic sensory impairment (n = 1) and cervical myelopathy (n = 1). In TE there were electrophysiological changes consistent with a median large fibre neuropathic abnormality (mean compound muscle action potential difference -6.3 mV ([-9.3, -3.3], p = 0.0002) ([95% CI], p-value)) and reduced sympathetic skin response amplitudes (-0.8 mV ([-1.5, -0.2], p = 0.0089)) in the affected upper limbs. In the lower limbs there was evidence of sural nerve dysfunction (sensory nerve action potential -5.8 μV ([-10.7, -0.8], p = 0.0232)) and impaired warm perception thresholds (+3.0°C ([0.6, 5.4], p = 0.0169)).
We found a range of clinical features relevant to individuals with TE beyond upper limb compressive neuropathies supporting the need for a detailed neurological examination to exclude other treatable pathologies. The electrophysiological evidence of large and small fibre axonal nerve dysfunction in symptomatic and asymptomatic limbs may be a result of the original insult and merits further investigation.
海豹肢症是一种极其罕见的先天性畸形,是子宫内接触沙利度胺导致的一系列缺陷中的一种极端情况。有沙利度胺胚胎病(TE)的个体报告称,在成年后,发育不良的肢体出现了提示周围神经系统功能障碍的症状。
采用标准神经生理学测试,对患有上肢异常和神经病变症状的TE受试者与健康对照进行病例对照研究。在评估前排除周围神经病变的其他原因。
对17名TE受试者(年龄50.4±1.3[均值±标准差]岁,10名女性)和17名对照者(37.9±9.0岁;8名女性)进行临床检查,发现四分之三的受试者有上肢压迫性神经病变的特征。此外,检查结果提示下肢存在轻度感觉神经病变(n = 1)、L5神经根性感觉障碍(n = 1)和颈髓病(n = 1)。在TE患者中,电生理变化与正中大纤维神经病变异常一致(平均复合肌肉动作电位差异为-6.3 mV([-9.3, -3.3],p = 0.0002)([95%置信区间],p值)),且患侧上肢交感皮肤反应幅度降低(-0.8 mV([-1.5, -0.2],p = 0.0089))。在下肢,有腓肠神经功能障碍的证据(感觉神经动作电位为-5.8 μV([-10.7, -0.8],p = 0.0232))和温觉阈值受损(+3.0°C([0.6, 5.4],p = 0.0169))。
我们发现,除上肢压迫性神经病变外,TE患者还有一系列相关临床特征,这支持需要进行详细的神经系统检查以排除其他可治疗的病变。有症状和无症状肢体出现大、小纤维轴索性神经功能障碍的电生理证据可能是最初损伤的结果,值得进一步研究。