Tan Jin Ai Mary Anne, Kho Siew Leng, Ngim Chin Fang, Chua Kek Heng, Goh Ai Sim, Yeoh Seoh Leng, George Elizabeth
Department of Biomedical Science, Faculty of Medicine, University of Malaya, Kuala Lumpur, Malaysia.
Department of Paediatrics, School of Medicine and Health Sciences, Monash University Sunway Campus, Selangor, Malaysia.
Sci Rep. 2016 Jun 8;6:26994. doi: 10.1038/srep26994.
Haemoglobin (Hb) Adana (HBA2:c.179>A) interacts with deletional and nondeletional α-thalassaemia mutations to produce HbH disorders with varying clinical manifestations from asymptomatic to severe anaemia with significant hepatosplenomegaly. Hb Adana carriers are generally asymptomatic and haemoglobin subtyping is unable to detect this highly unstable α-haemoglobin variant. This study identified 13 patients with compound heterozygosity for Hb Adana with either the 3.7 kb gene deletion (-α(3.7)), Hb Constant Spring (HbCS) (HBA2:c.427T>C) or Hb Paksé (HBA2:429A>T). Multiplex Amplification Refractory Mutation System was used for the detection of five deletional and six nondeletional α-thalassaemia mutations. Duplex-PCR was used to confirm Hb Paksé and HbCS. Results showed 84.6% of the Hb Adana patients were Malays. Using DNA studies, compound heterozygosity for Hb Adana and HbCS (α(codon 59)α/α(CS)α) was confirmed in 11 patients. A novel point in this investigation was that DNA studies confirmed Hb Paksé for the first time in a Malaysian patient (α(codon 59)α/α(Paksé)α) after nine years of being misdiagnosis with Hb Adana and HbCS (α(codon 59)α/α(CS)α). Thus, the reliance on haematology studies and Hb subtyping to detect Hb variants is inadequate in countries where thalassaemia is prevalent and caused by a wide spectrum of mutations.
血红蛋白(Hb)阿达纳(HBA2:c.179>A)与缺失型和非缺失型α地中海贫血突变相互作用,产生临床表现各异的HbH疾病,从无症状到重度贫血并伴有明显肝脾肿大。Hb阿达纳携带者通常无症状,血红蛋白亚型分析无法检测到这种高度不稳定的α血红蛋白变异体。本研究确定了13例携带Hb阿达纳复合杂合子的患者,其分别伴有3.7 kb基因缺失(-α(3.7))、血红蛋白恒春(HbCS)(HBA2:c.427T>C)或血红蛋白巴色(Hb Paksé)(HBA2:429A>T)。采用多重扩增阻滞突变系统检测5种缺失型和6种非缺失型α地中海贫血突变。采用双重PCR法确认Hb Paksé和HbCS。结果显示,84.6%的Hb阿达纳患者为马来人。通过DNA研究,在11例患者中证实了Hb阿达纳和HbCS的复合杂合子(α(密码子59)α/α(CS)α)。本研究的一个新发现是,一名马来西亚患者在被误诊为Hb阿达纳和HbCS(α(密码子59)α/α(CS)α)9年后,DNA研究首次证实其携带Hb Paksé(α(密码子59)α/α(Paksé)α)。因此,在地中海贫血流行且由多种突变引起的国家,仅依靠血液学研究和血红蛋白亚型分析来检测血红蛋白变异体是不够的。