Rukavina Katarina, Töpper Rudolf, Kunze Alexandra, Hess Alexander, Glatzel Markus, Valdueza Jose Manuel, Farschtschi Said, Hagel Christian
Institute of Neuropathology, University Medical Center Hamburg-Eppendorf, Hamburg, Germany; Department of Gerontopsychiatry, Asklepios Klinik Nord, Ochsenzoll, Hamburg, Germany.
Department of Neurology, Asklepios Klinik Harburg, Hamburg, Germany.
Eur J Med Genet. 2019 Oct;62(10):103710. doi: 10.1016/j.ejmg.2019.103710. Epub 2019 Jul 4.
Neurofibromatosis type 1 (NF1) is an autosomal dominant neurocutaneous disorder, characterized by cafe-au-lait macules, benign neurofibromas as well as malignant peripheral nerve sheath tumours, freckling in the axillary or inguinal regions, optic glioma and Lisch nodules (iris hamartomas) and further manifestations like bone deformities etc. Additionally, NF1 patients are at increased risk of early-onset cerebrovascular diseases, the pathogenesis of which has not been clarified yet. Here we report the first case of two siblings with NF1 who suffered an acute ischemic stroke. Professionals treating NF1 patients should be aware of the elevated risk of stroke in this population. Large prospective studies are needed to establish optimal guidelines for diagnosis, monitoring and treatment of cerebrovascular disease in patients suffering from NF1, as well as to achieve a consensus on routine vascular screening in NF1.
1型神经纤维瘤病(NF1)是一种常染色体显性神经皮肤疾病,其特征为咖啡斑、良性神经纤维瘤以及恶性外周神经鞘瘤、腋窝或腹股沟区雀斑、视神经胶质瘤和Lisch结节(虹膜错构瘤),还有诸如骨骼畸形等其他表现。此外,NF1患者发生早发性脑血管疾病的风险增加,其发病机制尚未阐明。在此,我们报告首例患有NF1的两例同胞发生急性缺血性卒中的病例。治疗NF1患者的专业人员应意识到该人群中卒中风险升高。需要开展大型前瞻性研究,以制定针对NF1患者脑血管疾病的诊断、监测和治疗的最佳指南,并就NF1患者的常规血管筛查达成共识。