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更正:杜氏肌营养不良症可步行患者中,具有适合跳跃外显子44、45、51和53的突变的长期自然史数据。

Correction: Long-term natural history data in Duchenne muscular dystrophy ambulant patients with mutations amenable to skip exons 44, 45, 51 and 53.

作者信息

Brogna Claudia, Coratt Giorgia, Pane Marika, Ricotti Valeria, Messina Sonia, D'Amico Adele, Bruno Claudio, Vita Gianluca, Berardinelli Angela, Mazzone Elena, Magri Francesca, Ricci Federica, Mongini Tiziana, Battini Roberta, Bello Luca, Pegoraro Elena, Baranello Giovanni, Previtali Stefano C, Politano Luisa, Comi Giacomo P, Sansone Valeria A, Donati Alice, Bertini Enrico, Muntoni Francesco, Goemans Nathalie, Mercuri Eugenio

出版信息

PLoS One. 2019 Jul 31;14(7):e0220714. doi: 10.1371/journal.pone.0220714. eCollection 2019.

Abstract

[This corrects the article DOI: 10.1371/journal.pone.0218683.].

摘要

[本文更正了文章的数字对象标识符:10.1371/journal.pone.0218683。]

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