Department of Anatomy, Hainan Medical College, Haikou, Hainan, China.
Centre de Diagnostic Prénatal, Hôpital MFME, Fort de France, Martinique, France.
Hum Mutat. 2020 Dec;41(12):2167-2178. doi: 10.1002/humu.24132. Epub 2020 Nov 10.
Herein, we report the screening of a large panel of genes in a series of 80 fetuses with congenital heart defects (CHDs) and/or heterotaxy and no cytogenetic anomalies. There were 49 males (61%/39%), with a family history in 28 cases (35%) and no parental consanguinity in 77 cases (96%). All fetuses had complex CHD except one who had heterotaxy and midline anomalies while 52 cases (65%) had heterotaxy in addition to CHD. Altogether, 29 cases (36%) had extracardiac and extra-heterotaxy anomalies. A pathogenic variant was found in 10/80 (12.5%) cases with a higher percentage in the heterotaxy group (8/52 cases, 15%) compared with the non-heterotaxy group (2/28 cases, 7%), and in 3 cases with extracardiac and extra-heterotaxy anomalies (3/29, 10%). The inheritance was recessive in six genes (DNAI1, GDF1, MMP21, MYH6, NEK8, and ZIC3) and dominant in two genes (SHH and TAB2). A homozygous pathogenic variant was found in three cases including only one case with known consanguinity. In conclusion, after removing fetuses with cytogenetic anomalies, next-generation sequencing discovered a causal variant in 12.5% of fetal cases with CHD and/or heterotaxy. Genetic counseling for future pregnancies was greatly improved. Surprisingly, unexpected consanguinity accounts for 20% of cases with identified pathogenic variants.
在此,我们对 80 例患有先天性心脏病(CHD)和/或内脏转位且无细胞遗传学异常的胎儿进行了大量基因的筛选。其中男性 49 例(61%/39%),28 例(35%)有家族史,77 例(96%)无父母近亲结婚。除了 1 例有内脏转位和中线异常外,所有胎儿均患有复杂的 CHD,而 52 例(65%)除了 CHD 外还有内脏转位。共有 29 例(36%)有心脏外和内脏外异常。在 80 例病例中发现了 10 例(12.5%)致病性变异,其中内脏转位组(8/52 例,15%)高于非内脏转位组(2/28 例,7%),在 3 例有心脏外和内脏外异常的病例中(3/29,10%)也发现了致病性变异。6 个基因(DNAI1、GDF1、MMP21、MYH6、NEK8 和 ZIC3)的遗传方式为隐性,2 个基因(SHH 和 TAB2)的遗传方式为显性。在 3 例病例中发现了纯合致病性变异,其中仅 1 例有已知近亲结婚。总之,在去除有细胞遗传学异常的胎儿后,下一代测序在 12.5%的 CHD 和/或内脏转位胎儿中发现了一个致病变异。这大大改善了对未来妊娠的遗传咨询。令人惊讶的是,意外近亲结婚占已确定致病变异病例的 20%。