Protein Chemistry, Genentech Inc, San Francisco, California, USA.
Biochemical and Cellular Pharmacology, Genentech Inc, San Francisco, California, USA.
Protein Sci. 2021 Jun;30(6):1169-1183. doi: 10.1002/pro.4082. Epub 2021 Apr 26.
Despite the need to monitor the impact of Cancer Immunotherapy (CI)/Immuno-Oncology (IO) therapeutics on neoantigen-specific T-cell responses, very few clinical programs incorporate this aspect of immune monitoring due to the challenges in high-throughput (HTP) generation of Major Histocompatibility Complex Class I (MHCI) tetramers across a wide range of HLA alleles. This limitation was recently addressed through the development of MHCI complexes with peptides containing a nonnatural UV cleavable amino acid (conditional MHCI ligands) that enabled HTP peptide exchange upon UV exposure. Despite this advancement, the number of alleles with known conditional MHCI ligands is limited. We developed a novel workflow to enable identification and validation of conditional MHCI ligands across a range of HLA alleles. First, known peptide binders were screened via an enzyme-linked immunosorbent assay (ELISA) assay. Conditional MHCI ligands were designed using the highest-performing peptides and evaluated in the same ELISA assay. The top performers were then selected for scale-up production. Next-generation analytical techniques (LC/MS, SEC-MALS, and 2D LC/MS) were used to characterize the complex after refolding with the conditional MHCI ligands. Finally, we used 2D LC/MS to evaluate peptide exchange with these scaled-up conditional MHCI complexes after UV exposure with validated peptide binders. Successful peptide exchange was observed for all conditional MHCI ligands upon UV exposure, validating our screening approach. This approach has the potential to be broadly applied and enable HTP generation of MHCI monomers and tetramers across a wider range of HLA alleles, which could be critical to enabling the use of MHCI tetramers to monitor neoantigen-specific T-cells in the clinic.
尽管需要监测癌症免疫疗法(CI)/免疫肿瘤学(IO)治疗对新抗原特异性 T 细胞反应的影响,但由于在广泛的 HLA 等位基因范围内生成主要组织相容性复合物 I 类(MHCI)四聚体的高通量(HTP)存在挑战,很少有临床项目纳入这一免疫监测方面。最近,通过开发含有非天然 UV 可切割氨基酸的肽的 MHCI 复合物(条件性 MHCI 配体)来解决这一限制,该方法在 UV 暴露时能够实现 HTP 肽交换。尽管取得了这一进展,但具有已知条件性 MHCI 配体的等位基因数量有限。我们开发了一种新的工作流程,能够在一系列 HLA 等位基因中识别和验证条件性 MHCI 配体。首先,通过酶联免疫吸附测定(ELISA)筛选已知的肽结合物。使用表现最佳的肽设计条件性 MHCI 配体,并在相同的 ELISA 测定中进行评估。然后选择表现最佳的肽进行扩大生产。接下来使用下一代分析技术(LC/MS、SEC-MALS 和 2D LC/MS)对经条件性 MHCI 配体重折叠后的复合物进行表征。最后,我们使用 2D LC/MS 在经 UV 照射后用经验证的肽结合物评估这些扩大生产的条件性 MHCI 复合物的肽交换。所有条件性 MHCI 配体在 UV 照射下均观察到成功的肽交换,验证了我们的筛选方法。这种方法具有广泛应用的潜力,并能够在更广泛的 HLA 等位基因范围内生成 MHCI 单体和四聚体的 HTP,这对于使用 MHCI 四聚体在临床上监测新抗原特异性 T 细胞可能至关重要。