Service of Neurology, Hospital Sierrallana-IDIVAL, Torrelavega, Spain.
Department of Medicine and Psychiatry, University of Cantabria, Santander, Spain.
Front Immunol. 2021 Mar 25;12:614715. doi: 10.3389/fimmu.2021.614715. eCollection 2021.
The extended interval dosing (EID) of natalizumab has been suggested to be associated with a reduced risk of progressive multifocal leukoencephalopathy (PML) and short-term preservation of efficacy but its long-term effectiveness remain unknown. We aimed to determine the long-term effectiveness and safety of natalizumab in an EID setting in a cohort of patients with multiple sclerosis (MS) treated for more than 7 years. We conducted an observational retrospective cohort study, including 39 (34 female, 5 male) patients with clinically definite relapsing-MS, initially treated with standard interval dosing (SID) of natalizumab (mean time 54 months [SD29]) who were then switched to EID, every 8 weeks (mean time 76 months [SD13]). The main outcome measures included the following: i) annualized relapse rate (ARR), ii) radiological activity, iii) disability progression, and iv) NEDA-3 no evidence of disease activity index. EID preserved ARR, radiological activity, and prevented disability worsening during follow-up. The proportion of patients maintaining their NEDA-3 status after 24, 48, and 72 months of natalizumab administration in EID was 94%, 73%, and 70%, respectively. Stratified analysis according to history of drug therapy showed that the EID of natalizumab was slightly more effective in naïve patients than in those previously treated with other immunosuppressive drugs. No cases of PML or other severe adverse reactions were reported. In conclusion, long-term therapy with natalizumab in an EID setting following an SID regimen maintained its disease-modifying activity, and was safe and well tolerated for over 7 years. These encouraging observational results need to be confirmed in controlled clinical trials.
那他珠单抗的延长间隔给药(EID)已被证明与降低进行性多灶性白质脑病(PML)的风险和短期疗效保留有关,但长期疗效仍不清楚。我们旨在确定 EID 环境中那他珠单抗在接受治疗超过 7 年的多发性硬化症(MS)患者队列中的长期疗效和安全性。我们进行了一项观察性回顾性队列研究,包括 39 名(34 名女性,5 名男性)临床确诊的复发性 MS 患者,最初接受标准间隔给药(SID)那他珠单抗(平均时间 54 个月[29 个标准差]),然后转换为 EID,每 8 周(平均时间 76 个月[13 个标准差])。主要观察指标包括:i)年复发率(ARR),ii)放射学活动,iii)残疾进展,和 iv)NEDA-3 无疾病活动指数。EID 保留了 ARR、放射学活动,并在随访期间防止残疾恶化。在 EID 中接受那他珠单抗治疗 24、48 和 72 个月后,分别有 94%、73%和 70%的患者保持了 NEDA-3 状态。根据药物治疗史进行的分层分析表明,EID 那他珠单抗在初治患者中的效果略优于在先前接受其他免疫抑制剂治疗的患者。未报告 PML 或其他严重不良反应的病例。总之,在 SID 方案之后,EID 环境中使用那他珠单抗的长期治疗维持了其疾病修饰活性,并且在超过 7 年的时间内是安全且耐受良好的。这些令人鼓舞的观察结果需要在对照临床试验中得到证实。