Jibiki Takaharu, Nishimura Hayato, Sengoku Shintaro, Kodama Kota
Department of Innovation Science, School of Environment and Society, Tokyo Institute of Technology, Tokyo 108-0023, Japan.
Policy Planning Division, RIKEN, Saitama 351-0198, Japan.
Cancers (Basel). 2021 Jul 9;13(14):3448. doi: 10.3390/cancers13143448.
This study investigated a case of Memorial Sloan Kettering-Integrated Mutation Profiling of Actionable Cancer Targets (MSK-IMPACT), a tumor profiling test approved by the U.S. Food and Drug Administration (FDA) in 2017, to examine what factors would contribute to healthcare innovation. First, we set the following three parameters to observe cases: (i) the FDA regulatory reforms, (ii) early application of new technologies, such as next-generation sequencing (NGS), to both research and clinical settings, and (iii) accumulation of open data. Then, we performed a comparative analysis of MSK-IMPACT with FoundationOne CDx and Oncomine Dx Target Test, both of which were FDA-approved tumor profiling tests launched in 2017. As a result, we found that MSK-IMPACT secures neutrality as a non-profit organization, achieves the active incorporation of basic research results, and performs superiorly in clinical operations, such as patient enrollment. On the contrary, we confirmed that FoundationOne CDx was the most prominent case in terms of the number of new drugs and expanded indications approved in which the FDA's expedited approval programs were considerably utilized. Consequently, to uncover the full potential of MSK-IMPACT, it is suggested that more intersectoral collaborative activities between various healthcare stakeholders, in particular, pharmaceutical companies, for driving clinical development must be carried out based on an organizational framework that facilitates collaboration.
本研究调查了纪念斯隆凯特琳癌症中心可操作癌症靶点综合突变分析(MSK-IMPACT)的一个案例,这是一项肿瘤分析检测,于2017年获得美国食品药品监督管理局(FDA)批准,旨在研究哪些因素有助于医疗创新。首先,我们设定了以下三个参数来观察案例:(i)FDA监管改革;(ii)新技术(如下一代测序(NGS))在研究和临床环境中的早期应用;(iii)开放数据的积累。然后,我们将MSK-IMPACT与FoundationOne CDx和Oncomine Dx Target Test进行了比较分析,这两者都是2017年推出的经FDA批准的肿瘤分析检测。结果,我们发现MSK-IMPACT作为一个非营利组织确保了中立性,积极纳入基础研究成果,并且在临床操作(如患者招募)方面表现出色。相反,我们证实FoundationOne CDx在获批的新药数量和扩展适应症方面是最突出的案例,其中大量利用了FDA的加速批准计划。因此,为了挖掘MSK-IMPACT的全部潜力,建议在促进合作的组织框架基础上,各类医疗利益相关者,特别是制药公司之间开展更多跨部门合作活动,以推动临床开发。