McNamara Katherine L, Caswell-Jin Jennifer L, Joshi Rohan, Ma Zhicheng, Kotler Eran, Bean Gregory R, Kriner Michelle, Zhou Zoey, Hoang Margaret, Beechem Joseph, Zoeller Jason, Press Michael F, Slamon Dennis J, Hurvitz Sara A, Curtis Christina
Department of Medicine, Division of Oncology, Stanford University School of Medicine, Stanford, CA, USA.
Stanford Cancer Institute, Stanford University School of Medicine, Stanford, CA, USA.
Nat Cancer. 2021 Apr;2(4):400-413. doi: 10.1038/s43018-021-00190-z. Epub 2021 Apr 8.
The addition of HER2-targeted agents to neoadjuvant chemotherapy has dramatically improved pathological complete response (pCR) rates in early-stage, HER2-positive breast cancer. Nonetheless, up to 50% of patients have residual disease after treatment, while others are likely overtreated. Here, we performed multiplex spatial proteomic characterization of 122 samples from 57 HER2-positive breast tumors from the neoadjuvant TRIO-US B07 clinical trial sampled pre-treatment, after 14-21 d of HER2-targeted therapy and at surgery. We demonstrated that proteomic changes after a single cycle of HER2-targeted therapy aids the identification of tumors that ultimately undergo pCR, outperforming pre-treatment measures or transcriptomic changes. We further developed and validated a classifier that robustly predicted pCR using a single marker, CD45, measured on treatment, and showed that CD45-positive cell counts measured via conventional immunohistochemistry perform comparably. These results demonstrate robust biomarkers that can be used to enable the stratification of sensitive tumors early during neoadjuvant HER2-targeted therapy, with implications for tailoring subsequent therapy.
在新辅助化疗中添加HER2靶向药物显著提高了早期HER2阳性乳腺癌的病理完全缓解(pCR)率。尽管如此,仍有高达50%的患者在治疗后有残留疾病,而其他患者可能接受了过度治疗。在此,我们对来自新辅助TRIO-US B07临床试验的57例HER2阳性乳腺肿瘤的122个样本进行了多重空间蛋白质组学表征,这些样本在治疗前、HER2靶向治疗14 - 21天后以及手术时进行采样。我们证明,单周期HER2靶向治疗后的蛋白质组学变化有助于识别最终实现pCR的肿瘤,其性能优于治疗前的指标或转录组变化。我们进一步开发并验证了一种分类器,该分类器使用治疗时测量的单一标志物CD45能够可靠地预测pCR,并表明通过传统免疫组织化学测量的CD45阳性细胞计数表现相当。这些结果证明了强大的生物标志物可用于在新辅助HER2靶向治疗早期对敏感肿瘤进行分层,这对定制后续治疗具有重要意义。