Department of Hematology, Hemotherapy and Cell Therapy, University of São Paulo (USP), São Paulo, Brazil.
Laboratory of Medical Investigation in Pathogenesis and Directed Therapy in Onco-Immuno-Hematology (LIM-31), University of São Paulo (USP), Avenue Dr Enéas de Carvalho Aguiar, 155, Ambulatory Building, 1st. Floor, Room 61, Cerqueira César, São Paulo, 05403-000, Brazil.
Clin Epigenetics. 2022 Dec 19;14(1):180. doi: 10.1186/s13148-022-01395-4.
Nodal mature T-cell lymphomas (nMTCL) comprises a heterogeneous group of rare malignancies with aggressive biological behavior and poor prognosis. Epigenetic phenomena, including mutations in genes that control DNA methylation and histone deacetylation, in addition to inactivating mutations in the RhoA GTPase, play a central role in its pathogenesis and constitute potential new targets for therapeutic intervention. Tumor mutational burden (TMB) reflects the process of clonal evolution, predicts response to anti-cancer therapies and has emerged as a prognostic biomarker in several solid neoplasms; however, its potential prognostic impact remains unknown in nMTCL. In this study, we conducted Sanger sequencing of formalin-fixed paraffin-embedded (FFPE) diagnostic tumor samples using a target-panel to search for recurrent mutations involving the IDH-1/IDH-2, TET-2, DNMT3A and RhoA genes in 59 cases of nMTCL. For the first time, we demonstrated that high-TMB, defined by the presence of ≥ two mutations involving the aforementioned genes, was associated with decreased overall survival in nMTCL patients treated with CHOP-like regimens. Additionally, high-TMB was correlated with bulky disease, lower overall response rate, and higher mortality. Future studies using larger cohorts may validate our preliminary results that indicate TMB as a potential molecular biomarker associated with adverse prognosis in nMTCL.
结内成熟 T 细胞淋巴瘤(nMTCL)是一组具有侵袭性生物学行为和不良预后的罕见恶性肿瘤,其具有异质性。表观遗传现象,包括控制 DNA 甲基化和组蛋白去乙酰化的基因的突变,以及 RhoA GTPase 的失活突变,在其发病机制中起核心作用,并构成潜在的治疗干预新靶点。肿瘤突变负担(TMB)反映了克隆进化的过程,预测对癌症治疗的反应,并已成为几种实体肿瘤的预后生物标志物;然而,其在 nMTCL 中的潜在预后影响尚不清楚。在这项研究中,我们使用靶向面板对 59 例 nMTCL 的福尔马林固定石蜡包埋(FFPE)诊断肿瘤样本进行了 Sanger 测序,以寻找涉及 IDH-1/IDH-2、TET-2、DNMT3A 和 RhoA 基因的复发性突变。我们首次证明,在接受 CHOP 样方案治疗的 nMTCL 患者中,存在≥两种涉及上述基因的突变的高-TMB 与总生存期降低相关。此外,高-TMB 与肿块性疾病、总体反应率降低和死亡率升高相关。使用更大队列的未来研究可能会验证我们的初步结果,即 TMB 作为与 nMTCL 不良预后相关的潜在分子生物标志物。