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Valoctocogene roxaparvovec gene transfer in participants with HIV.

作者信息

Ragni Margaret V, Majerus Elaine, Fong Sylvia, Yates Bridget, Scheeler Stephen, Razon Lisa, Yu Hua, Reddy Divya B, Robinson Tara M

机构信息

Medicine and Clinical and Translational Science, Department of Medicine, Division Hematology/Oncology, University of Pittsburgh Medical Center, Hemophilia Center of Western Pennsylvania, Pittsburgh, PA.

Department of Medicine, Washington University in St. Louis, St. Louis, MO.

出版信息

Blood Adv. 2023 Apr 25;7(8):1525-1530. doi: 10.1182/bloodadvances.2022008948.

Abstract
摘要
https://cdn.ncbi.nlm.nih.gov/pmc/blobs/c972/10130610/6b94d1da295a/BLOODA_ADV-2022-008948-gr1a.jpg

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Multiyear Factor VIII Expression after AAV Gene Transfer for Hemophilia A.
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6
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