Suppr超能文献

ART 前遗传学中的伦理学:一例漏诊的 X 连锁 Menkes 病。

Ethics in pre-ART genetics: a missed X-linked Menkes disease case.

机构信息

Department of Genetics, Copenhagen University Hospital, Rigshospital, Copenhagen, Denmark.

出版信息

J Assist Reprod Genet. 2023 Apr;40(4):811-816. doi: 10.1007/s10815-023-02778-z. Epub 2023 Mar 30.

Abstract

Assisted reproductive technology (ART) has experienced dramatic progress over the last 30 years, and gamete donation is routine in fertility clinics. Major advances in genetic diagnostics are part of this development due to the ability to analyze multiple genes or whole genomes fast and to an affordable prize. This requires knowledge and capability to evaluate genetic variants correctly in a clinical setting. Here we report a Menkes disease case, born after ART, where genetic screening and variant scoring failed to identify an egg donor as carrier of this fatal X-linked disorder. The gene variant is a deletion of a single base pair leading to a frameshift and premature termination of the protein, predicted to result in no or severely diminished function. The variant would be classified as likely pathogenic (class 4) and should be readily detectable by molecular genetic screening techniques. We wish to highlight this case to prevent future similar cases. IVI Igenomix has developed and embarked on an ambitious screening program to detect and prevent a large number of inherited severe childhood disorders in ART pregnancies. The company has recently achieved ISO 15189 certification with competence to evaluate and deliver timely, accurate, and reliable results. Failure to identify a pathogenic variant in the ATP7A gene leading to birth of two boys with Menkes disease invokes the required procedures to screen and detect disease-causing gene variants. This calls for ethical and legal considerations in ART diagnostics to prevent fatal errors like the present.

摘要

辅助生殖技术(ART)在过去 30 年中经历了巨大的进步,配子捐赠在生育诊所中已成为常规。由于能够快速且以可承受的价格分析多个基因或整个基因组,遗传诊断学的重大进展是这一发展的一部分。这需要在临床环境中正确评估遗传变异的知识和能力。在这里,我们报告了一例 Menkes 病病例,该病例是在 ART 后出生的,遗传筛查和变异评分未能确定卵子捐赠者是这种致命的 X 连锁疾病的携带者。该基因变异是单个碱基对的缺失,导致移码和蛋白质过早终止,预计会导致无功能或严重减少的功能。该变异将被归类为可能致病(类别 4),并且应该可以通过分子遗传筛选技术轻松检测到。我们希望突出这个案例,以防止未来出现类似的情况。IVI Igenomix 已经开发并启动了一项雄心勃勃的筛选计划,以检测和预防 ART 妊娠中大量遗传性严重儿童疾病。该公司最近已通过 ISO 15189 认证,具有评估和提供及时、准确和可靠结果的能力。未能在 ATP7A 基因中识别出导致两名 Menkes 病男孩出生的致病性变异,引发了筛选和检测致病基因变异的必要程序。这就需要在 ART 诊断中进行伦理和法律考虑,以防止像现在这样的致命错误。

https://cdn.ncbi.nlm.nih.gov/pmc/blobs/66d4/10224873/42df66158c66/10815_2023_2778_Fig1_HTML.jpg

文献AI研究员

20分钟写一篇综述,助力文献阅读效率提升50倍。

立即体验

用中文搜PubMed

大模型驱动的PubMed中文搜索引擎

马上搜索

文档翻译

学术文献翻译模型,支持多种主流文档格式。

立即体验